Literature DB >> 24691177

Repairing without cutting: a safer alternative to gene correction?

Fulvio Mavilio1.   

Abstract

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Year:  2014        PMID： 24691177      PMCID： PMC3982485          DOI： 10.1038/mt.2014.40

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  13 in total

Review 1.  Inherited epidermolysis bullosa: recent basic and clinical advances.

Authors:  Jo-David Fine
Journal:  Curr Opin Pediatr       Date:  2010-08       Impact factor: 2.856

2.  Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery.

Authors:  Angelo Lombardo; Pietro Genovese; Christian M Beausejour; Silvia Colleoni; Ya-Li Lee; Kenneth A Kim; Dale Ando; Fyodor D Urnov; Cesare Galli; Philip D Gregory; Michael C Holmes; Luigi Naldini
Journal:  Nat Biotechnol       Date:  2007-10-28       Impact factor: 54.908

Review 3.  Mechanisms of retroviral integration and mutagenesis.

Authors:  Alessia Cavazza; Arianna Moiani; Fulvio Mavilio
Journal:  Hum Gene Ther       Date:  2013-02       Impact factor: 5.695

4.  Efficient KRT14 targeting and functional characterization of transplanted human keratinocytes for the treatment of epidermolysis bullosa simplex.

Authors:  Lisa M Petek; Philip Fleckman; Daniel G Miller
Journal:  Mol Ther       Date:  2010-06-22       Impact factor: 11.454

5.  AAV-mediated gene targeting methods for human cells.

Authors:  Iram F Khan; Roli K Hirata; David W Russell
Journal:  Nat Protoc       Date:  2011-03-24       Impact factor: 13.491

6.  Engineering of human pluripotent stem cells by AAV-mediated gene targeting.

Authors:  Iram F Khan; Roli K Hirata; Pei-Rong Wang; Yi Li; Jordan Kho; Angel Nelson; Yunwen Huo; Maja Zavaljevski; Carol Ware; David W Russell
Journal:  Mol Ther       Date:  2010-04-20       Impact factor: 11.454

7.  Site-specific integration and tailoring of cassette design for sustainable gene transfer.

Authors:  Angelo Lombardo; Daniela Cesana; Pietro Genovese; Bruno Di Stefano; Elena Provasi; Daniele F Colombo; Margherita Neri; Zulma Magnani; Alessio Cantore; Pietro Lo Riso; Martina Damo; Oscar M Pello; Michael C Holmes; Philip D Gregory; Angela Gritti; Vania Broccoli; Chiara Bonini; Luigi Naldini
Journal:  Nat Methods       Date:  2011-08-21       Impact factor: 28.547

8.  Correction of laminin-5 deficiency in human epidermal stem cells by transcriptionally targeted lentiviral vectors.

Authors:  Francesca Di Nunzio; Giulietta Maruggi; Stefano Ferrari; Enzo Di Iorio; Valentina Poletti; Marta Garcia; Marcela Del Rio; Michele De Luca; Fernando Larcher; Graziella Pellegrini; Fulvio Mavilio
Journal:  Mol Ther       Date:  2008-09-23       Impact factor: 11.454

Review 9.  ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering.

Authors:  Thomas Gaj; Charles A Gersbach; Carlos F Barbas
Journal:  Trends Biotechnol       Date:  2013-05-09       Impact factor: 19.536

10.  Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells.

Authors:  Fulvio Mavilio; Graziella Pellegrini; Stefano Ferrari; Francesca Di Nunzio; Enzo Di Iorio; Alessandra Recchia; Giulietta Maruggi; Giuliana Ferrari; Elena Provasi; Chiara Bonini; Sergio Capurro; Andrea Conti; Cristina Magnoni; Alberto Giannetti; Michele De Luca
Journal:  Nat Med       Date:  2006-11-19       Impact factor: 53.440
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  1 in total

Review 1.  Research Techniques Made Simple: The Application of CRISPR-Cas9 and Genome Editing in Investigative Dermatology.

Authors:  Joan Ramon Guitart; Jodi L Johnson; Wade W Chien
Journal:  J Invest Dermatol       Date:  2016-09       Impact factor: 8.551
  1 in total

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