Literature DB >> 24493206

Ophthalmic findings in an infant with phosphomannomutase deficiency.

Wyatt B Messenger1, Paul Yang, Mark E Pennesi.   

Abstract

INTRODUCTION: We present the ocular features including full-field electroretinography (ff-ERG) and spectral domain optical coherence tomography (SD-OCT) in a 14-month-old infant with congenital disorder of glycosylation type 1a (PMM2-CDG). METHODS AND
RESULTS: An infant with failure to thrive, bilateral neurosensory hearing loss, cerebellar hypoplasia, and pericardial effusions was referred to ophthalmic genetics for evaluation. The patient had fix and follow vision, an intermittent esotropia, moderate myopia, a hypo pigmented macula, and mild attenuation of the retinal vasculature. Electroretinography showed severe reduction in both rod and cone-dependent responses with a negative waveform pattern. Handheld SD-OCT revealed severe attenuation of the outer retina throughout the macula, but with preservation of outer retinal structures in the fovea.
CONCLUSION: PMM2-CDG is a rare congenital disorder for which both ff-ERG and SD-OCT were useful in demonstrating early changes in retinal architecture and function.

Entities:  

Mesh:

Substances:

Year:  2014        PMID: 24493206      PMCID: PMC3990245          DOI: 10.1007/s10633-014-9427-0

Source DB:  PubMed          Journal:  Doc Ophthalmol        ISSN: 0012-4486            Impact factor:   2.379


  14 in total

1.  ISCEV Standard for full-field clinical electroretinography (2008 update).

Authors:  M F Marmor; A B Fulton; G E Holder; Y Miyake; M Brigell; M Bach
Journal:  Doc Ophthalmol       Date:  2008-11-22       Impact factor: 2.379

Review 2.  Congenital disorders of glycosylation (CDG): it's (nearly) all in it!

Authors:  Jaak Jaeken
Journal:  J Inherit Metab Dis       Date:  2011-03-08       Impact factor: 4.982

3.  Retinal characteristics of the congenital disorder of glycosylation PMM2-CDG.

Authors:  Dorothy A Thompson; Ruth J Lyons; Isabelle Russell-Eggitt; Alki Liasis; Herbert Jägle; Stephanie Grünewald
Journal:  J Inherit Metab Dis       Date:  2013-02-22       Impact factor: 4.982

4.  Mutations in PMM2, a phosphomannomutase gene on chromosome 16p13, in carbohydrate-deficient glycoprotein type I syndrome (Jaeken syndrome).

Authors:  G Matthijs; E Schollen; E Pardon; M Veiga-Da-Cunha; J Jaeken; J J Cassiman; E Van Schaftingen
Journal:  Nat Genet       Date:  1997-05       Impact factor: 38.330

5.  The 'dark' side of sedation: 12 years of office-based pediatric deep sedation for electroretinography in the dark.

Authors:  Kirk Lalwani; Brian D Tompkins; Kevin Burnes; Melissa R Krahmer; Mark E Pennesi; Richard G Weleber
Journal:  Paediatr Anaesth       Date:  2011-01       Impact factor: 2.556

Review 6.  Phosphomannomutase deficiency: the molecular basis of the classical Jaeken syndrome (CDGS type Ia).

Authors:  G Matthijs; E Schollen; L Heykants; S Grünewald
Journal:  Mol Genet Metab       Date:  1999-10       Impact factor: 4.797

7.  Evolution of ophthalmic and electrophysiological findings in identical twin sisters with the carbohydrate deficient glycoprotein syndrome type 1 over a period of 14 years.

Authors:  I Casteels; W Spileers; A Leys; L Lagae; J Jaeken
Journal:  Br J Ophthalmol       Date:  1996-10       Impact factor: 4.638

Review 8.  Congenital disorders of glycosylation.

Authors:  J Jaeken; G Matthijs
Journal:  Annu Rev Genomics Hum Genet       Date:  2001       Impact factor: 8.929

9.  Ophthalmic manifestations of congenital disorder of glycosylation type 1a.

Authors:  Hanne Jensen; Susanne Kjaergaard; Flemming Klie; H U Moller
Journal:  Ophthalmic Genet       Date:  2003-06       Impact factor: 1.803

10.  Long-term characterization of retinal degeneration in rd1 and rd10 mice using spectral domain optical coherence tomography.

Authors:  Mark E Pennesi; Keith V Michaels; Sienna S Magee; Anastasiya Maricle; Sean P Davin; Anupam K Garg; Michael J Gale; Daniel C Tu; Yuquan Wen; Laura R Erker; Peter J Francis
Journal:  Invest Ophthalmol Vis Sci       Date:  2012-07-10       Impact factor: 4.799

View more
  5 in total

1.  PMM2-CDG and sensorineural hearing loss.

Authors:  Çiğdem Seher Kasapkara; Zeren Barış; Mustafa Kılıç; Deniz Yüksel; Lies Keldermans; Gert Matthijs; Jaak Jaeken
Journal:  J Inherit Metab Dis       Date:  2017-07-31       Impact factor: 4.982

2.  Ophthalmological and electrophysiological findings in monozygotic twin sisters with phosphomannomutase 2 deficiency (PMM2-CDG) over a period of 37 years.

Authors:  Ines Van Hees; Jaak Jaeken; Wouter Meersseman; Ingele Casteels
Journal:  GMS Ophthalmol Cases       Date:  2019-11-20

3.  A Dpagt1 Missense Variant Causes Degenerative Retinopathy without Myasthenic Syndrome in Mice.

Authors:  Lillian F Hyde; Yang Kong; Lihong Zhao; Sriganesh Ramachandra Rao; Jieping Wang; Lisa Stone; Andrew Njaa; Gayle B Collin; Mark P Krebs; Bo Chang; Steven J Fliesler; Patsy M Nishina; Jürgen K Naggert
Journal:  Int J Mol Sci       Date:  2022-10-09       Impact factor: 6.208

4.  Cerebral Blood Flow Alterations in High Myopia: An Arterial Spin Labeling Study.

Authors:  Huihui Wang; Shanshan Li; Xi Chen; Yanling Wang; Jing Li; Zhenchang Wang
Journal:  Neural Plast       Date:  2020-01-09       Impact factor: 3.599

5.  An ERG and OCT study of neuronal ceroid lipofuscinosis CLN2 Battens retinopathy.

Authors:  Dorothy A Thompson; Siân E Handley; Robert H Henderson; Oliver R Marmoy; Paul Gissen
Journal:  Eye (Lond)       Date:  2021-07-16       Impact factor: 3.775

  5 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.