Literature DB >> 23449105

Transplantation of gene-corrected motor neurons as a therapeutic strategy for spinal muscular atrophy.

Kathrin Meyer1, Carlos J Miranda, Brian K Kaspar.   

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Year:  2013        PMID： 23449105      PMCID： PMC3642289          DOI： 10.1038/mt.2013.23

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  13 in total

Review 1.  Progress and prospects: targeted gene alteration (TGA).

Authors:  H Parekh-Olmedo; E B Kmiec
Journal:  Gene Ther       Date:  2007-11-01       Impact factor: 5.250

Review 2.  Advances in targeted genome editing.

Authors:  Pablo Perez-Pinera; David G Ousterout; Charles A Gersbach
Journal:  Curr Opin Chem Biol       Date:  2012-07-20       Impact factor: 8.822

3.  Rapid and efficient generation of functional motor neurons from human pluripotent stem cells using gene delivered transcription factor codes.

Authors:  Mark E Hester; Matthew J Murtha; SungWon Song; Meghan Rao; Carlos J Miranda; Kathrin Meyer; Jinbin Tian; Gabriella Boulting; David V Schaffer; Michael X Zhu; Samuel L Pfaff; Fred H Gage; Brian K Kaspar
Journal:  Mol Ther       Date:  2011-07-19       Impact factor: 11.454

4.  SMNDelta7, the major product of the centromeric survival motor neuron (SMN2) gene, extends survival in mice with spinal muscular atrophy and associates with full-length SMN.

Authors:  Thanh T Le; Lan T Pham; Matthew E R Butchbach; Honglai L Zhang; Umrao R Monani; Daniel D Coovert; Tatiana O Gavrilina; Lei Xing; Gary J Bassell; Arthur H M Burghes
Journal:  Hum Mol Genet       Date:  2005-02-09       Impact factor: 6.150

5.  Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy.

Authors:  Stefania Corti; Monica Nizzardo; Chiara Simone; Marianna Falcone; Martina Nardini; Dario Ronchi; Chiara Donadoni; Sabrina Salani; Giulietta Riboldi; Francesca Magri; Giorgia Menozzi; Clara Bonaglia; Federica Rizzo; Nereo Bresolin; Giacomo P Comi
Journal:  Sci Transl Med       Date:  2012-12-19       Impact factor: 17.956

6.  Histological and functional benefit following transplantation of motor neuron progenitors to the injured rat spinal cord.

Authors:  Sharyn L Rossi; Gabriel Nistor; Tanya Wyatt; Hong Zhen Yin; Aleksandra J Poole; John H Weiss; Matthew J Gardener; Sipke Dijkstra; David F Fischer; Hans S Keirstead
Journal:  PLoS One       Date:  2010-07-29       Impact factor: 3.240

7.  Induced pluripotent stem cells from a spinal muscular atrophy patient.

Authors:  Allison D Ebert; Junying Yu; Ferrill F Rose; Virginia B Mattis; Christian L Lorson; James A Thomson; Clive N Svendsen
Journal:  Nature       Date:  2008-12-21       Impact factor: 49.962

8.  Embryonic stem cell-derived neural stem cells improve spinal muscular atrophy phenotype in mice.

Authors:  Stefania Corti; Monica Nizzardo; Martina Nardini; Chiara Donadoni; Sabrina Salani; Dario Ronchi; Chiara Simone; Marianna Falcone; Dimitra Papadimitriou; Federica Locatelli; Nicoletta Mezzina; Francesca Gianni; Nereo Bresolin; Giacomo P Comi
Journal:  Brain       Date:  2009-12-23       Impact factor: 13.501

9.  Human motor neuron progenitor transplantation leads to endogenous neuronal sparing in 3 models of motor neuron loss.

Authors:  Tanya J Wyatt; Sharyn L Rossi; Monica M Siegenthaler; Jennifer Frame; Rockelle Robles; Gabriel Nistor; Hans S Keirstead
Journal:  Stem Cells Int       Date:  2011-05-23       Impact factor: 5.443

10.  Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN.

Authors:  Kevin D Foust; Xueyong Wang; Vicki L McGovern; Lyndsey Braun; Adam K Bevan; Amanda M Haidet; Thanh T Le; Pablo R Morales; Mark M Rich; Arthur H M Burghes; Brian K Kaspar
Journal:  Nat Biotechnol       Date:  2010-02-28       Impact factor: 68.164
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