Literature DB >> 21289636

Solving the problem of γ-retroviral vectors containing long terminal repeats.

Derek A Persons1, Christopher Baum.   

Abstract

Mesh：

Year:  2011        PMID： 21289636      PMCID： PMC3034864          DOI： 10.1038/mt.2010.305

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   11.454


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  16 in total

1.  Physiological promoters reduce the genotoxic risk of integrating gene vectors.

Authors:  Daniela Zychlinski; Axel Schambach; Ute Modlich; Tobias Maetzig; Johann Meyer; Elke Grassman; Anjali Mishra; Christopher Baum
Journal:  Mol Ther       Date:  2008-03-04       Impact factor: 11.454

2.  Stem-cell gene therapy for the Wiskott-Aldrich syndrome.

Authors:  Kaan Boztug; Manfred Schmidt; Adrian Schwarzer; Pinaki P Banerjee; Inés Avedillo Díez; Ricardo A Dewey; Marie Böhm; Ali Nowrouzi; Claudia R Ball; Hanno Glimm; Sonja Naundorf; Klaus Kühlcke; Rainer Blasczyk; Irina Kondratenko; László Maródi; Jordan S Orange; Christof von Kalle; Christoph Klein
Journal:  N Engl J Med       Date:  2010-11-11       Impact factor: 91.245

3.  Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

Authors:  Marion G Ott; Manfred Schmidt; Kerstin Schwarzwaelder; Stefan Stein; Ulrich Siler; Ulrike Koehl; Hanno Glimm; Klaus Kühlcke; Andrea Schilz; Hana Kunkel; Sonja Naundorf; Andrea Brinkmann; Annette Deichmann; Marlene Fischer; Claudia Ball; Ingo Pilz; Cynthia Dunbar; Yang Du; Nancy A Jenkins; Neal G Copeland; Ursula Lüthi; Moustapha Hassan; Adrian J Thrasher; Dieter Hoelzer; Christof von Kalle; Reinhard Seger; Manuel Grez
Journal:  Nat Med       Date:  2006-04-02       Impact factor: 53.440

4.  Efficient construction of producer cell lines for a SIN lentiviral vector for SCID-X1 gene therapy by concatemeric array transfection.

Authors:  Robert E Throm; Annastasia A Ouma; Sheng Zhou; Anantharaman Chandrasekaran; Timothy Lockey; Michael Greene; Suk See De Ravin; Morvarid Moayeri; Harry L Malech; Brian P Sorrentino; John T Gray
Journal:  Blood       Date:  2009-03-13       Impact factor: 22.113

5.  LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1.

Authors:  S Hacein-Bey-Abina; C Von Kalle; M Schmidt; M P McCormack; N Wulffraat; P Leboulch; A Lim; C S Osborne; R Pawliuk; E Morillon; R Sorensen; A Forster; P Fraser; J I Cohen; G de Saint Basile; I Alexander; U Wintergerst; T Frebourg; A Aurias; D Stoppa-Lyonnet; S Romana; I Radford-Weiss; F Gross; F Valensi; E Delabesse; E Macintyre; F Sigaux; J Soulier; L E Leiva; M Wissler; C Prinz; T H Rabbitts; F Le Deist; A Fischer; M Cavazzana-Calvo
Journal:  Science       Date:  2003-10-17       Impact factor: 47.728

6.  The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy.

Authors:  Eugenio Montini; Daniela Cesana; Manfred Schmidt; Francesca Sanvito; Cynthia C Bartholomae; Marco Ranzani; Fabrizio Benedicenti; Lucia Sergi Sergi; Alessandro Ambrosi; Maurilio Ponzoni; Claudio Doglioni; Clelia Di Serio; Christof von Kalle; Luigi Naldini
Journal:  J Clin Invest       Date:  2009-03-23       Impact factor: 14.808

7.  Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy.

Authors:  Alessandro Aiuti; Barbara Cassani; Grazia Andolfi; Massimiliano Mirolo; Luca Biasco; Alessandra Recchia; Fabrizia Urbinati; Cristina Valacca; Samantha Scaramuzza; Memet Aker; Shimon Slavin; Matteo Cazzola; Daniela Sartori; Alessandro Ambrosi; Clelia Di Serio; Maria Grazia Roncarolo; Fulvio Mavilio; Claudio Bordignon
Journal:  J Clin Invest       Date:  2007-08       Impact factor: 14.808

8.  Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration.

Authors:  Eugenio Montini; Daniela Cesana; Manfred Schmidt; Francesca Sanvito; Maurilio Ponzoni; Cynthia Bartholomae; Lucia Sergi Sergi; Fabrizio Benedicenti; Alessandro Ambrosi; Clelia Di Serio; Claudio Doglioni; Christof von Kalle; Luigi Naldini
Journal:  Nat Biotechnol       Date:  2006-05-28       Impact factor: 54.908

9.  Self-inactivating gammaretroviral vectors for gene therapy of X-linked severe combined immunodeficiency.

Authors:  Susannah I Thornhill; Axel Schambach; Steven J Howe; Meera Ulaganathan; Elke Grassman; David Williams; Bernhard Schiedlmeier; Neil J Sebire; H Bobby Gaspar; Christine Kinnon; Christopher Baum; Adrian J Thrasher
Journal:  Mol Ther       Date:  2008-01-08       Impact factor: 11.454

10.  Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients.

Authors:  Steven J Howe; Marc R Mansour; Kerstin Schwarzwaelder; Cynthia Bartholomae; Michael Hubank; Helena Kempski; Martijn H Brugman; Karin Pike-Overzet; Stephen J Chatters; Dick de Ridder; Kimberly C Gilmour; Stuart Adams; Susannah I Thornhill; Kathryn L Parsley; Frank J T Staal; Rosemary E Gale; David C Linch; Jinhua Bayford; Lucie Brown; Michelle Quaye; Christine Kinnon; Philip Ancliff; David K Webb; Manfred Schmidt; Christof von Kalle; H Bobby Gaspar; Adrian J Thrasher
Journal:  J Clin Invest       Date:  2008-09       Impact factor: 14.808
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  16 in total

Review 1.  Safe harbours for the integration of new DNA in the human genome.

Authors:  Michel Sadelain; Eirini P Papapetrou; Frederic D Bushman
Journal:  Nat Rev Cancer       Date:  2011-12-01       Impact factor: 60.716

2.  Clinical Utilization of Chimeric Antigen Receptor T Cells in B Cell Acute Lymphoblastic Leukemia: An Expert Opinion from the European Society for Blood and Marrow Transplantation and the American Society for Blood and Marrow Transplantation.

Authors:  Ankit J Kansagra; Noelle V Frey; Merav Bar; Theodore W Laetsch; Paul A Carpenter; Bipin N Savani; Helen E Heslop; Catherine M Bollard; Krishna V Komanduri; Dennis A Gastineau; Christian Chabannon; Miguel A Perales; Michael Hudecek; Mahmoud Aljurf; Leslie Andritsos; John A Barrett; Veronika Bachanova; Chiara Bonini; Armin Ghobadi; Saar I Gill; Joshua Hill; Saad Kenderian; Partow Kebriaei; Arnon Nagler; David Maloney; Hien D Liu; Nirali N Shah; Mohamed A Kharfan-Dabaja; Elizabeth J Shpall; Ghulam J Mufti; Laura Johnston; Elad Jacoby; Ali Bazarbachi; John F DiPersio; Steven Z Pavletic; David L Porter; Stephan A Grupp; Michel Sadelain; Mark R Litzow; Mohamad Mohty; Shahrukh K Hashmi
Journal:  Biol Blood Marrow Transplant       Date:  2018-12-18       Impact factor: 5.742

Review 3.  Center for fetal monkey gene transfer for heart, lung, and blood diseases: an NHLBI resource for the gene therapy community.

Authors:  Alice F Tarantal; Sonia I Skarlatos
Journal:  Hum Gene Ther       Date:  2012-10-19       Impact factor: 5.695

Review 4.  Biosafety features of lentiviral vectors.

Authors:  Axel Schambach; Daniela Zychlinski; Birgitta Ehrnstroem; Christopher Baum
Journal:  Hum Gene Ther       Date:  2013-02       Impact factor: 5.695

5.  Ubiquitous high-level gene expression in hematopoietic lineages provides effective lentiviral gene therapy of murine Wiskott-Aldrich syndrome.

Authors:  Alexander Astrakhan; Blythe D Sather; Byoung Y Ryu; Socheath Khim; Swati Singh; Stephanie Humblet-Baron; Hans D Ochs; Carol H Miao; David J Rawlings
Journal:  Blood       Date:  2012-03-19       Impact factor: 22.113

6.  Clinical utilization of Chimeric Antigen Receptor T-cells (CAR-T) in B-cell acute lymphoblastic leukemia (ALL)-an expert opinion from the European Society for Blood and Marrow Transplantation (EBMT) and the American Society for Blood and Marrow Transplantation (ASBMT).

Authors:  Ankit J Kansagra; Noelle V Frey; Merav Bar; Theodore W Laetsch; Paul A Carpenter; Bipin N Savani; Helen E Heslop; Catherine M Bollard; Krishna V Komanduri; Dennis A Gastineau; Christian Chabannon; Miguel A Perales; Michael Hudecek; Mahmoud Aljurf; Leslie Andritsos; John A Barrett; Veronika Bachanova; Chiara Bonini; Armin Ghobadi; Saar I Gill; Joshua A Hill; Saad Kenderian; Partow Kebriaei; Arnon Nagler; David Maloney; Hien D Liu; Nirali N Shah; Mohamed A Kharfan-Dabaja; Elizabeth J Shpall; Ghulam J Mufti; Laura Johnston; Elad Jacoby; Ali Bazarbachi; John F DiPersio; Steven Z Pavletic; David L Porter; Stephan A Grupp; Michel Sadelain; Mark R Litzow; Mohamad Mohty; Shahrukh K Hashmi
Journal:  Bone Marrow Transplant       Date:  2019-05-15       Impact factor: 5.483

Review 7.  The role of induced pluripotent stem cells in research and therapy of primary immunodeficiencies.

Authors:  Katja G Weinacht; Patrick M Brauer; Kerstin Felgentreff; Alex Devine; Andrew R Gennery; Silvia Giliani; Waleed Al-Herz; Axel Schambach; Juan Carlos Zúñiga-Pflücker; Luigi D Notarangelo
Journal:  Curr Opin Immunol       Date:  2012-07-25       Impact factor: 7.486

8.  Scale-up and manufacturing of clinical-grade self-inactivating γ-retroviral vectors by transient transfection.

Authors:  J C M van der Loo; W P Swaney; E Grassman; A Terwilliger; T Higashimoto; A Schambach; C Baum; A J Thrasher; D A Williams; D L Nordling; L Reeves; P Malik
Journal:  Gene Ther       Date:  2011-07-14       Impact factor: 5.250

9.  Prevention of Lethal Murine Hypophosphatasia by Neonatal Ex Vivo Gene Therapy Using Lentivirally Transduced Bone Marrow Cells.

Authors:  Osamu Iijima; Koichi Miyake; Atsushi Watanabe; Noriko Miyake; Tsutomu Igarashi; Chizu Kanokoda; Aki Nakamura-Takahashi; Hideaki Kinoshita; Taku Noguchi; Shinichi Abe; Sonoko Narisawa; José Luis Millán; Takashi Okada; Takashi Shimada
Journal:  Hum Gene Ther       Date:  2015-11-19       Impact factor: 5.695

10.  Challenges in vector and trial design using retroviral vectors for long-term gene correction in hematopoietic stem cell gene therapy.

Authors:  Jacqueline Corrigan-Curay; Odile Cohen-Haguenauer; Marina O'Reilly; Susan R Ross; Hung Fan; Naomi Rosenberg; Nikunj Somia; Nancy King; Theodore Friedmann; Cynthia Dunbar; Alessandro Aiuti; Luigi Naldini; Christopher Baum; Christof von Kalle; Hans-Peter Kiem; Eugenio Montini; Frederic Bushman; Brian P Sorrentino; Manuel Carrondo; Harry Malech; Gösta Gahrton; Robyn Shapiro; Linda Wolff; Eugene Rosenthal; Robert Jambou; John Zaia; Donald B Kohn
Journal:  Mol Ther       Date:  2012-06       Impact factor: 11.454
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