Literature DB >> 21051233

The risks of therapeutic misconception and individual patient (n=1) "trials" in rare diseases such as Duchenne dystrophy.

Annemieke Aartsma-Rus1.   

Abstract

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Mesh：

Year:  2010        PMID： 21051233     DOI： 10.1016/j.nmd.2010.09.012

Source DB:  PubMed          Journal:  Neuromuscul Disord        ISSN： 0960-8966            Impact factor:   4.296


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  6 in total

Review 1.  Challenges posed to the European pharmaceutical regulatory system by highly personalized medicines.

Authors:  John D Johnston; Peter Feldschreiber
Journal:  Br J Clin Pharmacol       Date:  2014-03       Impact factor: 4.335

Review 2.  Ethics in pharmacologic research in the child with a disability.

Authors:  Peter Rumney; James A Anderson; Stephen E Ryan
Journal:  Paediatr Drugs       Date:  2015-02       Impact factor: 3.022

3.  Quantitative MRI and loss of free ambulation in Duchenne muscular dystrophy.

Authors:  Arne Fischmann; Patricia Hafner; Monika Gloor; Maurice Schmid; Andrea Klein; Urs Pohlman; Tanja Waltz; Rocio Gonzalez; Tanja Haas; Oliver Bieri; Dirk Fischer
Journal:  J Neurol       Date:  2012-11-09       Impact factor: 4.849

4.  Raising Awareness of Therapeutic Misconception and Optimism Around Clinical Trials in Huntington's Disease.

Authors:  Susanne Tamara de Bot
Journal:  J Huntingtons Dis       Date:  2019

5.  Stakeholder perspectives on clinical research related to therapies for rare diseases: therapeutic misconception and the value of research.

Authors:  Kylie Tingley; Doug Coyle; Ian D Graham; Pranesh Chakraborty; Kumanan Wilson; Beth K Potter
Journal:  Orphanet J Rare Dis       Date:  2021-01-12       Impact factor: 4.123

6.  Guidance in social and ethical issues related to clinical, diagnostic care and novel therapies for hereditary neuromuscular rare diseases: "translating" the translational.

Authors:  Pauline McCormack; Simon Woods; Annemieke Aartsma-Rus; Lynn Hagger; Agnes Herczegfalvi; Emma Heslop; Joseph Irwin; Janbernd Kirschner; Patrick Moeschen; Francesco Muntoni; Marie-Christine Ouillade; Jes Rahbek; Christoph Rehmann-Sutter; Francoise Rouault; Thomas Sejersen; Elizabeth Vroom; Volker Straub; Kate Bushby; Alessandra Ferlini
Journal:  PLoS Curr       Date:  2013-01-10
  6 in total

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