Literature DB >> 9420542

Methylmalonic acidemia, cobalamin C type, presenting with cutaneous manifestations.

R Howard1, I J Frieden, D Crawford, T McCalmont, M L Levy, D S Rosenblatt, L Sweetman, S I Goodman, C Ohnstad, K Hart, M Berrios, S Packman.   

Abstract

BACKGROUND: Erosive dermatitis resembling the skin lesions of acrodermatitis enteropathica has been described in a number of aminoacidopathies and organic acidemias. In some, the dermatitis is a manifestation of untreated disease, while in others, including methylmalonic acidemia, skin lesions have been ascribed to nutritional deficiency due to therapeutic amino acid restrictions. OBSERVATIONS: We report 2 cases of methylmalonic acidemia presenting with cutaneous manifestations in the perinatal period before restrictive nutritional interventions. The cutaneous involvement consisted of cheilitis and diffuse erythema with erosions and desquamation. Methylmalonic acidemia, cobalamin C type, was subsequently diagnosed in both cases.
CONCLUSIONS: An erosive, desquamating dermatitis with histopathologic characteristics resembling acrodermatitis enteropathica may be a presenting sign in cobalamin C methylmalonic acidemia, even in the absence of long-standing nutritional restrictions or deficiency.

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Year:  1997        PMID: 9420542

Source DB:  PubMed          Journal:  Arch Dermatol        ISSN: 0003-987X


  7 in total

1.  Progressive neurological deterioration and MRI changes in cblC methylmalonic acidaemia treated with hydroxocobalamin.

Authors:  G M Enns; A J Barkovich; D S Rosenblatt; D R Fredrick; K Weisiger; C Ohnstad; S Packman
Journal:  J Inherit Metab Dis       Date:  1999-06       Impact factor: 4.982

Review 2.  Combined methylmalonic acidemia and homocystinuria, cblC type. II. Complications, pathophysiology, and outcomes.

Authors:  Nuria Carrillo-Carrasco; Charles P Venditti
Journal:  J Inherit Metab Dis       Date:  2011-07-12       Impact factor: 4.982

3.  Skin lesions in a patient with Cobalamin C disease in poor metabolic control.

Authors:  Pankaj Prasun; Cristel Chapel-Crespo; Amy Williamson; Paul Chu; Kimihiko Oishi; George Diaz
Journal:  J Inherit Metab Dis       Date:  2017-11-02       Impact factor: 4.982

4.  Methylmalonic aciduria presenting with recurrent multiple molluscum contagiosum lesions.

Authors:  Motonobu Nakamura; Yoshiki Tokura
Journal:  Dermatoendocrinol       Date:  2010-04

Review 5.  Guidelines for diagnosis and management of the cobalamin-related remethylation disorders cblC, cblD, cblE, cblF, cblG, cblJ and MTHFR deficiency.

Authors:  Martina Huemer; Daria Diodato; Bernd Schwahn; Manuel Schiff; Anabela Bandeira; Jean-Francois Benoist; Alberto Burlina; Roberto Cerone; Maria L Couce; Angeles Garcia-Cazorla; Giancarlo la Marca; Elisabetta Pasquini; Laura Vilarinho; James D Weisfeld-Adams; Viktor Kožich; Henk Blom; Matthias R Baumgartner; Carlo Dionisi-Vici
Journal:  J Inherit Metab Dis       Date:  2016-11-30       Impact factor: 4.982

6.  Acrodermatitis dysmetabolica as a sign of methylmalonic aciduria decompensation.

Authors:  Joana Rosa; Ana Beatriz Fraga; Rita de Carvalho; Ana Lúcia Maia; Ana Luísa Rodrigues; Maria Fernanda Gomes
Journal:  Clin Case Rep       Date:  2018-04-14

7.  Dementia, diarrhea, desquamating shellac-like dermatitis revealing late-onset cobalamin C deficiency.

Authors:  Robert Christopher Gilson; Luke Wallis; Jenny Yeh; Robert T Gilson
Journal:  JAAD Case Rep       Date:  2017-12-20
  7 in total

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