Authors: Pippa Staps; William B Rizzo; Frédéric M Vaz; Marianna Bugiani; Martin Giera; Bram Heijs; Antoine H C van Kampen; Mia L Pras-Raves; Marjolein Breur; Annemieke Groen; Sacha Ferdinandusse; Marinette van der Graaf; Gert Van Goethem; Martin Lammens; Ron A Wevers; Michèl A A P Willemsen Journal: J Inherit Metab Dis Date: 2020-07-09 Impact factor: 4.982