Authors: Christiaan P Sentner; Irene J Hoogeveen; David A Weinstein; René Santer; Elaine Murphy; Patrick J McKiernan; Ulrike Steuerwald; Nicholas J Beauchamp; Joanna Taybert; Pascal Laforêt; François M Petit; Aurélie Hubert; Philippe Labrune; G Peter A Smit; Terry G J Derks Journal: J Inherit Metab Dis Date: 2016-04-22 Impact factor: 4.982