Authors: Karl Heinz Weiss; Mart Van de Moortele; Daniel Nils Gotthardt; Jan Pfeiffenberger; Jessica Seessle; Elena Ullrich; Evelien Gielen; Herman Borghs; Els Adriaens; Wolfgang Stremmel; Wouter Meersseman; Steven Boonen; David Cassiman Journal: J Inherit Metab Dis Date: 2015-02-07 Impact factor: 4.982