Literature DB >> 36099921

The long road traveled in hematopoietic stem cell gene therapy.

David A Williams1.   

Abstract

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Year:  2022        PMID： 36099921      PMCID： PMC9552808          DOI： 10.1016/j.ymthe.2022.08.022

Source DB:  PubMed          Journal:  Mol Ther        ISSN： 1525-0016            Impact factor:   12.910


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  7 in total

1.  Introduction of a selectable gene into primitive stem cells capable of long-term reconstitution of the hemopoietic system of W/Wv mice.

Authors:  J E Dick; M C Magli; D Huszar; R A Phillips; A Bernstein
Journal:  Cell       Date:  1985-08       Impact factor: 41.582

Review 2.  Role of intergenic human gamma-delta-globin sequences in human hemoglobin switching and reactivation of fetal hemoglobin in adult erythroid cells.

Authors:  Arthur Bank; David O'Neill; Rocio Lopez; Dianne Pulte; Maureen Ward; Simon Mantha; Christine Richardson
Journal:  Ann N Y Acad Sci       Date:  2005       Impact factor: 5.691

3.  Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia.

Authors:  Marina Cavazzana-Calvo; Emmanuel Payen; Olivier Negre; Gary Wang; Kathleen Hehir; Floriane Fusil; Julian Down; Maria Denaro; Troy Brady; Karen Westerman; Resy Cavallesco; Beatrix Gillet-Legrand; Laure Caccavelli; Riccardo Sgarra; Leila Maouche-Chrétien; Françoise Bernaudin; Robert Girot; Ronald Dorazio; Geert-Jan Mulder; Axel Polack; Arthur Bank; Jean Soulier; Jérôme Larghero; Nabil Kabbara; Bruno Dalle; Bernard Gourmel; Gérard Socie; Stany Chrétien; Nathalie Cartier; Patrick Aubourg; Alain Fischer; Kenneth Cornetta; Frédéric Galacteros; Yves Beuzard; Eliane Gluckman; Frederick Bushman; Salima Hacein-Bey-Abina; Philippe Leboulch
Journal:  Nature       Date:  2010-09-16       Impact factor: 49.962

4.  Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.

Authors:  Sunita Goyal; John Tisdale; Manfred Schmidt; Julie Kanter; Jennifer Jaroscak; Dustin Whitney; Hans Bitter; Philip D Gregory; Geoffrey Parsons; Marianna Foos; Ashish Yeri; Maple Gioia; Sarah B Voytek; Alex Miller; Jessie Lynch; Richard A Colvin; Melissa Bonner
Journal:  N Engl J Med       Date:  2021-12-12       Impact factor: 91.245

5.  Introduction of new genetic material into pluripotent haematopoietic stem cells of the mouse.

Authors:  D A Williams; I R Lemischka; D G Nathan; R C Mulligan
Journal:  Nature       Date:  1984 Aug 9-15       Impact factor: 49.962

6.  A modified γ-retrovirus vector for X-linked severe combined immunodeficiency.

Authors:  Salima Hacein-Bey-Abina; Sung-Yun Pai; H Bobby Gaspar; Myriam Armant; Charles C Berry; Stephane Blanche; Jack Bleesing; Johanna Blondeau; Helen de Boer; Karen F Buckland; Laure Caccavelli; Guilhem Cros; Satiro De Oliveira; Karen S Fernández; Dongjing Guo; Chad E Harris; Gregory Hopkins; Leslie E Lehmann; Annick Lim; Wendy B London; Johannes C M van der Loo; Nirav Malani; Frances Male; Punam Malik; M Angélica Marinovic; Anne-Marie McNicol; Despina Moshous; Benedicte Neven; Matías Oleastro; Capucine Picard; Jerome Ritz; Christine Rivat; Axel Schambach; Kit L Shaw; Eric A Sherman; Leslie E Silberstein; Emmanuelle Six; Fabien Touzot; Alla Tsytsykova; Jinhua Xu-Bayford; Christopher Baum; Frederic D Bushman; Alain Fischer; Donald B Kohn; Alexandra H Filipovich; Luigi D Notarangelo; Marina Cavazzana; David A Williams; Adrian J Thrasher
Journal:  N Engl J Med       Date:  2014-10-09       Impact factor: 91.245

7.  Uncovering and dissecting the genotoxicity of self-inactivating lentiviral vectors in vivo.

Authors:  Daniela Cesana; Marco Ranzani; Monica Volpin; Cynthia Bartholomae; Caroline Duros; Alexandre Artus; Stefania Merella; Fabrizio Benedicenti; Lucia Sergi Sergi; Francesca Sanvito; Chiara Brombin; Alessandro Nonis; Clelia Di Serio; Claudio Doglioni; Christof von Kalle; Manfred Schmidt; Odile Cohen-Haguenauer; Luigi Naldini; Eugenio Montini
Journal:  Mol Ther       Date:  2014-01-20       Impact factor: 11.454
  7 in total

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