Literature DB >> 36042959

Variability in Serum Concentrations and Clinical Response in Artisanal Versus Pharmaceutical Cannabidiol Treatment of Pediatric Pharmacoresistant Epilepsy.

Nathan T Cohen1, Burak Bahar2, Joan A Conry1, John M Schreiber1.   

Abstract

OBJECTIVE: We hypothesized that serum cannabidiol (CBD) concentrations would be higher in patients taking pharmaceutical- versus artisanal-CBD oil, and higher serum CBD concentrations would correlate with increased side effects and decreased seizure frequency.
METHODS: This was a retrospective chart review. We included patients with pharmacoresistant epilepsy, treated with artisanal-CBD or pharmaceutical-CBD (Epidiolex), and with quantitative serum CBD concentrations. We tracked epilepsy diagnosis, artisanal-CBD dosage, pharmaceutical-CBD dose, serum CBD concentration, clobazam concentration, N-desmethylclobazam concentration, seizure history (frequency of motor seizures), response to medication (percentage reduction in motor seizures), and side effects.
RESULTS: Forty-two patients met inclusion criteria. Mean serum CBD concentration was 51.1 ng/mL (artisanal group) and 124 ng/mL (pharmaceutical group) (p = 0.022). Patients receiving artisanal-CBD had no change in median overall seizures (IQR, -50% to 50%); the pharmaceutical-CBD group had median 50% reduction (IQR, -90% to no change) (p = 0.199).
CONCLUSIONS: Pharmaceutical-CBD achieves higher serum CBD concentrations than artisanal-CBD in pediatric patients with refractory epilepsy. These higher CBD concentrations are associated with increased reported adverse effects, but no detectable difference in seizure frequency. Copyright. Pediatric Pharmacy Association. All rights reserved. For permissions, email: membership@pediatricpharmacy.org 2022.

Entities:  

Keywords:  Dravet syndrome; Epidiolex; Lennox-Gastaut syndrome; artisanal cannabidiol; cannabidiol; pediatric epilepsy

Year:  2022        PMID: 36042959      PMCID: PMC9400177          DOI: 10.5863/1551-6776-27.6.558

Source DB:  PubMed          Journal:  J Pediatr Pharmacol Ther        ISSN: 1551-6776


  19 in total

1.  Prospective evaluation of oral cannabis extracts in children with epilepsy.

Authors:  Kelly G Knupp; John D Rice; Laura J Helmkamp; Jeffrey Galinkin; Cristina Sempio; Klawitter Jost; Kevin E Chapman
Journal:  Seizure       Date:  2019-09-16       Impact factor: 3.184

2.  Purified Cannabidiol for Treatment of Refractory Epilepsies in Pediatric Patients with Developmental and Epileptic Encephalopathy.

Authors:  Nicola Pietrafusa; Alessandro Ferretti; Marina Trivisano; Luca de Palma; Costanza Calabrese; Giusy Carfì Pavia; Ilaria Tondo; Simona Cappelletti; Federico Vigevano; Nicola Specchio
Journal:  Paediatr Drugs       Date:  2019-08       Impact factor: 3.022

3.  Higher cannabidiol plasma levels are associated with better seizure response following treatment with a pharmaceutical grade cannabidiol.

Authors:  Jerzy P Szaflarski; Kathleen Hernando; E Martina Bebin; Tyler E Gaston; Leslie E Grayson; Steve B Ampah; Randall Moreadith
Journal:  Epilepsy Behav       Date:  2019-04-29       Impact factor: 2.937

4.  Cannabidiol in patients with treatment-resistant epilepsy: an open-label interventional trial.

Authors:  Orrin Devinsky; Eric Marsh; Daniel Friedman; Elizabeth Thiele; Linda Laux; Joseph Sullivan; Ian Miller; Robert Flamini; Angus Wilfong; Francis Filloux; Matthew Wong; Nicole Tilton; Patricia Bruno; Judith Bluvstein; Julie Hedlund; Rebecca Kamens; Jane Maclean; Srishti Nangia; Nilika Shah Singhal; Carey A Wilson; Anup Patel; Maria Roberta Cilio
Journal:  Lancet Neurol       Date:  2015-12-24       Impact factor: 44.182

5.  Drug-drug interaction between clobazam and cannabidiol in children with refractory epilepsy.

Authors:  Alexandra L Geffrey; Sarah F Pollack; Patricia L Bruno; Elizabeth A Thiele
Journal:  Epilepsia       Date:  2015-06-26       Impact factor: 5.864

Review 6.  Cannabinoids for epilepsy.

Authors:  David Gloss; Barbara Vickrey
Journal:  Cochrane Database Syst Rev       Date:  2014-03-05

7.  Antiepileptic drugs--best practice guidelines for therapeutic drug monitoring: a position paper by the subcommission on therapeutic drug monitoring, ILAE Commission on Therapeutic Strategies.

Authors:  Philip N Patsalos; David J Berry; Blaise F D Bourgeois; James C Cloyd; Tracy A Glauser; Svein I Johannessen; Ilo E Leppik; Torbjörn Tomson; Emilio Perucca
Journal:  Epilepsia       Date:  2008-07       Impact factor: 5.864

8.  Chronic administration of cannabidiol to healthy volunteers and epileptic patients.

Authors:  J M Cunha; E A Carlini; A E Pereira; O L Ramos; C Pimentel; R Gagliardi; W L Sanvito; N Lander; R Mechoulam
Journal:  Pharmacology       Date:  1980       Impact factor: 2.547

9.  Potential Clinical Benefits of CBD-Rich Cannabis Extracts Over Purified CBD in Treatment-Resistant Epilepsy: Observational Data Meta-analysis.

Authors:  Fabricio A Pamplona; Lorenzo Rolim da Silva; Ana Carolina Coan
Journal:  Front Neurol       Date:  2018-09-12       Impact factor: 4.003

10.  An Open Retrospective Study of a Standardized Cannabidiol Based-Oil in Treatment-Resistant Epilepsy.

Authors:  Francesca Marchese; Maria Stella Vari; Ganna Balagura; Antonella Riva; Vincenzo Salpietro; Alberto Verrotti; Rita Citraro; Simona Lattanzi; Carlo Minetti; Emilio Russo; Pasquale Striano
Journal:  Cannabis Cannabinoid Res       Date:  2020-07-21
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