Literature DB >> 35840676

CRISPR 'cousin' put to the test in landmark heart-disease trial.

Heidi Ledford.   

Abstract

Entities:  

Keywords:  CRISPR-Cas9 genome editing; Gene therapy; Medical research

Mesh:

Year:  2022        PMID: 35840676     DOI: 10.1038/d41586-022-01951-1

Source DB:  PubMed          Journal:  Nature        ISSN: 0028-0836            Impact factor:   69.504


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  2 in total

1.  In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates.

Authors:  Kiran Musunuru; Alexandra C Chadwick; Taiji Mizoguchi; Sara P Garcia; Jamie E DeNizio; Caroline W Reiss; Kui Wang; Sowmya Iyer; Chaitali Dutta; Victoria Clendaniel; Michael Amaonye; Aaron Beach; Kathleen Berth; Souvik Biswas; Maurine C Braun; Huei-Mei Chen; Thomas V Colace; John D Ganey; Soumyashree A Gangopadhyay; Ryan Garrity; Lisa N Kasiewicz; Jennifer Lavoie; James A Madsen; Yuri Matsumoto; Anne Marie Mazzola; Yusuf S Nasrullah; Joseph Nneji; Huilan Ren; Athul Sanjeev; Madeleine Shay; Mary R Stahley; Steven H Y Fan; Ying K Tam; Nicole M Gaudelli; Giuseppe Ciaramella; Leslie E Stolz; Padma Malyala; Christopher J Cheng; Kallanthottathil G Rajeev; Ellen Rohde; Andrew M Bellinger; Sekar Kathiresan
Journal:  Nature       Date:  2021-05-19       Impact factor: 69.504

2.  In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels.

Authors:  Tanja Rothgangl; Melissa K Dennis; Paulo J C Lin; Rurika Oka; Dominik Witzigmann; Lukas Villiger; Weihong Qi; Martina Hruzova; Lucas Kissling; Daniela Lenggenhager; Costanza Borrelli; Sabina Egli; Nina Frey; Noëlle Bakker; John A Walker; Anastasia P Kadina; Denis V Victorov; Martin Pacesa; Susanne Kreutzer; Zacharias Kontarakis; Andreas Moor; Martin Jinek; Drew Weissman; Markus Stoffel; Ruben van Boxtel; Kevin Holden; Norbert Pardi; Beat Thöny; Johannes Häberle; Ying K Tam; Sean C Semple; Gerald Schwank
Journal:  Nat Biotechnol       Date:  2021-05-19       Impact factor: 54.908

  2 in total

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