Literature DB >> 35706735

Comparing the Safety and Efficacy of L-Glutamine, Voxelotor, and Crizanlizumab for Reducing the Frequency of Vaso-Occlusive Crisis in Sickle Cell Disease: A Systematic Review.

Maurice H Dick1,2, Arowa Abdelgadir3, Vaishnavi Vijaya Kulkarni4, Hamna Akram3, Abanti Chatterjee5, Sushil Pokhrel3, Safeera Khan3.   

Abstract

Sickle cell disease (SCD) is a group of inherited red blood cell disorders affecting millions worldwide. The median life expectancy of someone with SCD remains significantly low despite improvements in standards of care and the implementation of hydroxyurea therapy. Notably, a 20-year interval existed (after the implementation of hydroxyurea therapy) prior to the approval of other sickle cell medications, namely, l-glutamine, voxelotor, and crizanlizumab. In this systematic review, these new medications' impact on the occurrences of vaso-occlusive crisis (VOC) events were analyzed and the adverse events of each were noted. Further, a secondary analysis was conducted to determine the effect of combination therapies, whether synergistic, antagonistic, or additive. The systematic review was conducted following the PRISMA 2020 guidelines. The effect-based and dose-effect-based approaches were utilized to determine the combined drugs combination index based on the recommended dosage to achieve an efficacy of 50%. L-glutamine and crizanlizumab were effective in reducing the frequency of VOC (p= 0.0216 and p = 0.02). Voxelotor effect on the reduction of VOC occurrences was not significant, however, its effect on increasing hemoglobin levels was significant (p= <0.001). In all three therapies, pain was the most common adverse event reported by participants. The analysis of combination therapies revealed that voxelotor plus l-glutamine was synergistic, voxelotor plus crizanlizumab was antagonistic, and l-glutamine plus crizanlizumab was additive. Thus, voxelotor plus l-glutamine combination therapy may be more beneficial to sickle cell disease patients. As such, robust combination drug studies for approved therapies used in SCD should be initiated with a specific focus on voxelotor plus l-glutamine. Additionally, the development of medications that lessen the pain burden in sickle cell disease patients should also be prioritized.
Copyright © 2022, Dick et al.

Entities:  

Keywords:  combination therapy; crizanlizumab; l-glutamine; sickle cell; vaso-occlusive crisis; voxelotor

Year:  2022        PMID: 35706735      PMCID: PMC9187358          DOI: 10.7759/cureus.24920

Source DB:  PubMed          Journal:  Cureus        ISSN: 2168-8184


  28 in total

1.  Severe infusion-related reaction to crizanlizumab in an adolescent with sickle cell disease.

Authors:  Kristine Karkoska; Charles T Quinn; Kelly Clapp; Patrick T McGann
Journal:  Am J Hematol       Date:  2020-09-30       Impact factor: 10.047

2.  Case series of patients with severe sickle cell disease treated with voxelotor (GBT440) by compassionate access.

Authors:  Gershwin Blyden; Kenneth R Bridges; Lanetta Bronte
Journal:  Am J Hematol       Date:  2018-05-12       Impact factor: 10.047

3.  Sudden death in sickle cell disease: current experience.

Authors:  Chijioke Nze; Brooke Fortin; Revital Freedman; Elyse Mandell; Maneka Puligandla; Donna Neuberg; Maureen Achebe
Journal:  Br J Haematol       Date:  2019-12-05       Impact factor: 6.998

Review 4.  The vaso-occlusive pain crisis in sickle cell disease: Definition, pathophysiology, and management.

Authors:  Deepika S Darbari; Vivien A Sheehan; Samir K Ballas
Journal:  Eur J Haematol       Date:  2020-05-19       Impact factor: 2.997

5.  First case of DRESS (drug reaction with eosinophilia and systemic symptoms) associated with voxelotor.

Authors:  Matthew Lee; Thomas Stringer; Jack Jacob; Elana M Friedman; Caterina Minniti; Henny H Billett; Susanna A Curtis
Journal:  Am J Hematol       Date:  2021-09-14       Impact factor: 13.265

6.  Trends in Sickle Cell Disease-Related Mortality in the United States, 1979 to 2017.

Authors:  Amanda B Payne; Jason M Mehal; Christina Chapman; Dana L Haberling; Lisa C Richardson; Christopher J Bean; W Craig Hooper
Journal:  Ann Emerg Med       Date:  2020-09       Impact factor: 5.721

7.  Voxelotor treatment of a patient with sickle cell disease and very severe anemia.

Authors:  Arun S Shet; Laurel Mendelsohn; Julia Harper; David Ostrowski; Eric R Henry; Eveline Gwaabe; Jim Nichols; Abdu I Alayash; William A Eaton; Swee Lay Thein
Journal:  Am J Hematol       Date:  2019-01-08       Impact factor: 10.047

8.  Management of Chronic Pain in Adults Living With Sickle Cell Disease in the Era of the Opioid Epidemic: A Qualitative Study.

Authors:  Cynthia B Sinha; Nitya Bakshi; Diana Ross; Lakshmanan Krishnamurti
Journal:  JAMA Netw Open       Date:  2019-05-03

9.  Impact of voxelotor (GBT440) on unconjugated bilirubin and jaundice in sickle cell disease.

Authors:  Paul Telfer; Irene Agodoa; Kathleen M Fox; Laurie Burke; Timothy Mant; Marzena Jurek; Margaret Tonda; Josh Lehrer-Graiwer
Journal:  Hematol Rep       Date:  2018-05-22

Review 10.  Efficacy and safety of recently approved drugs for sickle cell disease: a review of clinical trials.

Authors:  Muhammad Ashar Ali; Asrar Ahmad; Hafsa Chaudry; Wajeeha Aiman; Sobia Aamir; Muhammad Yasir Anwar; Anam Khan
Journal:  Exp Hematol       Date:  2020-08-22       Impact factor: 3.084

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