Literature DB >> 35228704

SMA type 2 and 3 improvements over 2 years.

Ian Fyfe1.   

Abstract

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Year:  2022        PMID: 35228704     DOI: 10.1038/s41582-022-00640-x

Source DB:  PubMed          Journal:  Nat Rev Neurol        ISSN: 1759-4758            Impact factor:   42.937


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  1 in total

1.  Nusinersen efficacy data for 24-month in type 2 and 3 spinal muscular atrophy.

Authors:  Marika Pane; Giorgia Coratti; Maria Carmela Pera; Valeria A Sansone; Sonia Messina; Adele d'Amico; Claudio Bruno; Francesca Salmin; Emilio Albamonte; Roberto De Sanctis; Maria Sframeli; Vincenzo Di Bella; Simone Morando; Concetta Palermo; Anna Lia Frongia; Laura Antonaci; Anna Capasso; Michela Catteruccia; Antonella Longo; Martina Ricci; Costanza Cutrona; Alice Pirola; Chiara Bravetti; Marina Pedemonte; Noemi Brolatti; Enrico Bertini; Eugenio Mercuri
Journal:  Ann Clin Transl Neurol       Date:  2022-02-15       Impact factor: 4.511

  1 in total

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