| Literature DB >> 35188328 |
Erica Lay1, Mahshid S Azamian1, Susan W Denfield2, William Dreyer2, Joseph A Spinner2, Debra Kearney3, Lilei Zhang1, Kim C Worley1, Weimin Bi1,4, Seema R Lalani1.
Abstract
Leiomodin-2 (LMOD2) is an important regulator of the thin filament length, known to promote elongation of actin through polymerization at pointed ends. Mice with Lmod2 deficiency die around 3 weeks of age due to severe dilated cardiomyopathy (DCM), resulting from decreased heart contractility due to shorter thin filaments. To date, there have been three infants from two families reported with biallelic variants in LMOD2, presenting with perinatal onset DCM. Here, we describe a third family with a child harboring a previously described homozygous frameshift variant, c.1243_1244delCT (p.L415Vfs*108) with DCM, presenting later in infancy at 9 months of age. Family history was relevant for a sibling who died suddenly at 1 year of age after being diagnosed with cardiomegaly. LMOD2-related cardiomyopathy is a rare form of inherited cardiomyopathy resulting from thin filament length dysregulation and should be considered in genetic evaluation of newborns and infants with suspected autosomal recessive inheritance or sporadic early onset cardiomyopathy.Entities:
Keywords: LMOD2; autosomal recessive disease; dilated cardiomyopathy; loss of function variant; short thin filament length
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Year: 2022 PMID: 35188328 PMCID: PMC9117498 DOI: 10.1002/ajmg.a.62699
Source DB: PubMed Journal: Am J Med Genet A ISSN: 1552-4825 Impact factor: 2.578