Literature DB >> 35145310

A solid start for gene therapy in Tay-Sachs disease.

Timothy W Yu1,2,3,4, Olaf Bodamer5,6,7.   

Abstract

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Year:  2022        PMID: 35145310     DOI: 10.1038/s41591-022-01687-5

Source DB:  PubMed          Journal:  Nat Med        ISSN: 1078-8956            Impact factor:   53.440


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  1 in total

1.  AAV gene therapy for Tay-Sachs disease.

Authors:  Terence R Flotte; Oguz Cataltepe; Ajit Puri; Ana Rita Batista; Richard Moser; Diane McKenna-Yasek; Catherine Douthwright; Gwladys Gernoux; Meghan Blackwood; Christian Mueller; Phillip W L Tai; Xuntian Jiang; Scot Bateman; Spiro G Spanakis; Julia Parzych; Allison M Keeler; Aly Abayazeed; Saurabh Rohatgi; Laura Gibson; Robert Finberg; Bruce A Barton; Zeynep Vardar; Mohammed Salman Shazeeb; Matthew Gounis; Cynthia J Tifft; Florian S Eichler; Robert H Brown; Douglas R Martin; Heather L Gray-Edwards; Miguel Sena-Esteves
Journal:  Nat Med       Date:  2022-02-10       Impact factor: 87.241

  1 in total

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