Literature DB >> 35075290

Gene therapy goes the distance in Wiskott-Aldrich syndrome.

Alessandra Biffi1,2.   

Abstract

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Year:  2022        PMID: 35075290     DOI: 10.1038/s41591-021-01653-7

Source DB:  PubMed          Journal:  Nat Med        ISSN: 1078-8956            Impact factor:   53.440


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  1 in total

1.  Retrieval of vector integration sites from cell-free DNA.

Authors:  Andrea Calabria; Laura Rudilosso; Daniela Cesana; Pierangela Gallina; Fabrizio Benedicenti; Giulio Spinozzi; Giulia Schiroli; Alessandra Magnani; Serena Acquati; Francesca Fumagalli; Valeria Calbi; Maximilian Witzel; Frederic D Bushman; Alessio Cantore; Pietro Genovese; Christoph Klein; Alain Fischer; Marina Cavazzana; Emmanuelle Six; Alessandro Aiuti; Luigi Naldini; Eugenio Montini
Journal:  Nat Med       Date:  2021-06-17       Impact factor: 87.241

  1 in total

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