Literature DB >> 34837429

NR2F1 database: 112 variants and 84 patients support refining the clinical synopsis of Bosch-Boonstra-Schaaf optic atrophy syndrome.

Benjamin Billiet1, Patrizia Amati-Bonneau2,3, Valérie Desquiret-Dumas2,3, Khadidja Guehlouz1, Dan Milea4, Philippe Gohier1, Guy Lenaers2, Delphine Mirebeau-Prunier2,3, Johan T den Dunnen5, Pascal Reynier2,3, Marc Ferré2.   

Abstract

Pathogenic variants of the nuclear receptor subfamily 2 group F member 1 gene (NR2F1) are responsible for Bosch-Boonstra-Schaaf optic atrophy syndrome (BBSOAS), an autosomal dominant disorder characterized by optic atrophy associated with developmental delay and intellectual disability, but with a clinical presentation which appears to be multifaceted. We created the first public locus-specific database dedicated to NR2F1. All variants and clinical cases reported in the literature, as well as new unpublished cases, were integrated into the database using standard nomenclature to describe both molecular and phenotypic anomalies. We subsequently pursued a comprehensive approach based on computed representation and analysis suggesting a refinement of the BBSOAS clinical description with respect to neurological features and the inclusion of additional signs of hypotonia and feeding difficulties. This database is fully accessible for both clinician and molecular biologists and should prove useful in further refining the clinical synopsis of NR2F1 as new data is recorded.
© 2021 Wiley Periodicals LLC.

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Keywords:  BBSOAS; Bosch-Boonstra-Schaaf optic atrophy syndrome; COUP transcription factor 1 protein; COUP-TF1; NR2F1; database; neurodegenerative disorders; nuclear receptor subfamily 2 group F member 1; ontology; optic atrophy

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Year:  2021        PMID: 34837429     DOI: 10.1002/humu.24305

Source DB:  PubMed          Journal:  Hum Mutat        ISSN: 1059-7794            Impact factor:   4.878


  2 in total

Review 1.  Pathophysiological Heterogeneity of the BBSOA Neurodevelopmental Syndrome.

Authors:  Michele Bertacchi; Chiara Tocco; Christian P Schaaf; Michèle Studer
Journal:  Cells       Date:  2022-04-08       Impact factor: 7.666

2.  Novel NR2F1 variant identified by whole-exome sequencing in a patient with Bosch-Boonstra-Schaaf optic atrophy syndrome.

Authors:  Ayca Kocaaga; Sevgi Yimenicioglu; Haluk Hüseyin Gürsoy
Journal:  Indian J Ophthalmol       Date:  2022-07       Impact factor: 2.969

  2 in total

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