| Literature DB >> 34837063 |
Ravi Savarirayan1, Penny Ireland2, Melita Irving3, Dominic Thompson4, Inês Alves5, Wagner A R Baratela6, James Betts7, Michael B Bober8, Silvio Boero9, Jenna Briddell8, Jeffrey Campbell8, Philippe M Campeau10, Patricia Carl-Innig11, Moira S Cheung3, Martyn Cobourne12, Valérie Cormier-Daire13, Muriel Deladure-Molla13, Mariana Del Pino14, Heather Elphick15, Virginia Fano14, Brigitte Fauroux13, Jonathan Gibbins3, Mari L Groves16, Lars Hagenäs17, Therese Hannon18, Julie Hoover-Fong16,19, Morrys Kaisermann20, Antonio Leiva-Gea21, Juan Llerena22, William Mackenzie8, Kenneth Martin23, Fabio Mazzoleni24, Sharon McDonnell18, Maria Costanza Meazzini25, Josef Milerad17, Klaus Mohnike26, Geert R Mortier27, Amaka Offiah15,28, Keiichi Ozono29, John A Phillips30, Steven Powell18, Yosha Prasad3, Cathleen Raggio31, Pablo Rosselli32, Judith Rossiter33, Angelo Selicorni34, Marco Sessa35, Mary Theroux8, Matthew Thomas18, Laura Trespedi36, David Tunkel16, Colin Wallis4, Michael Wright18, Natsuo Yasui37, Svein Otto Fredwall38,39.
Abstract
Achondroplasia, the most common skeletal dysplasia, is characterized by a variety of medical, functional and psychosocial challenges across the lifespan. The condition is caused by a common, recurring, gain-of-function mutation in FGFR3, the gene that encodes fibroblast growth factor receptor 3. This mutation leads to impaired endochondral ossification of the human skeleton. The clinical and radiographic hallmarks of achondroplasia make accurate diagnosis possible in most patients. However, marked variability exists in the clinical care pathways and protocols practised by clinicians who manage children and adults with this condition. A group of 55 international experts from 16 countries and 5 continents have developed consensus statements and recommendations that aim to capture the key challenges and optimal management of achondroplasia across each major life stage and sub-specialty area, using a modified Delphi process. The primary purpose of this first International Consensus Statement is to facilitate the improvement and standardization of care for children and adults with achondroplasia worldwide in order to optimize their clinical outcomes and quality of life.Entities:
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Year: 2021 PMID: 34837063 DOI: 10.1038/s41574-021-00595-x
Source DB: PubMed Journal: Nat Rev Endocrinol ISSN: 1759-5029 Impact factor: 47.564