Lindsay N Alfano1,2, Tahseen Mozaffar3,4. 1. Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA. 2. Department of Pediatrics, The Ohio State University, Columbus, OH, USA. 3. Department of Neurology, University of California, Irvine, CA, USA. 4. Department of Pathology and Laboratory Medicine, University of California, Irvine, CA, USA.
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