Literature DB >> 34626730

Comment on "Synthetic human ABCB4 mRNA therapy rescues severe liver disease phenotype in a BALB/c.Abcb4-/- mouse model of PFIC3".

Nicholas D Weber1, Javier Martínez-García2, Gloria González-Aseguinolaza3.   

Abstract

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Keywords:  Bile; Child; Cholestasis; Dependovirus; Genetic therapy; Liver Cirrhosis; Phospholipids; progressive familial intrahepatic 3

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Year:  2021        PMID: 34626730     DOI: 10.1016/j.jhep.2021.09.033

Source DB:  PubMed          Journal:  J Hepatol        ISSN: 0168-8278            Impact factor:   25.083


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  1 in total

Review 1.  Gene Therapy for Acquired and Genetic Cholestasis.

Authors:  Javier Martínez-García; Angie Molina; Gloria González-Aseguinolaza; Nicholas D Weber; Cristian Smerdou
Journal:  Biomedicines       Date:  2022-05-26
  1 in total

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