Literature DB >> 34404575

1st FSHD European Trial Network workshop:Working towards trial readiness across Europe.

N C Voermans1, M Vriens-Munoz Bravo2, G W Padberg3, P Laforêt4, N van Alfen, S Attarian, U A Badrising, P Bugiardini, P Camano González, R Y Carlier, I Desguerre, J Diaz-Manera, J Dumonceaux, B G van Engelen, T Evangelista, S Khosla, A Lópezde Munain, S M van der Maarel, A Mejat, M Monforte, F Montagnese, K Mul, P Oflazer, B Porter, S Quijano Roy, E Ricci, S Sacconi, V A Sansone, B Schoser, J Statland, E Stumpe, G Tasca, R Tawil, C Turner, J Vissing.   

Abstract

Entities:  

Keywords:  Biomarkers; Clinical outcome measures; FSHD; Imaging outcome measures; Trial readiness

Year:  2021        PMID: 34404575     DOI: 10.1016/j.nmd.2021.07.013

Source DB:  PubMed          Journal:  Neuromuscul Disord        ISSN: 0960-8966            Impact factor:   4.296


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  2 in total

1.  The predictive value of models of neuromuscular disorders to potentiate clinical translation.

Authors:  Maaike van Putten
Journal:  Dis Model Mech       Date:  2022-08-01       Impact factor: 5.732

Review 2.  Gene Editing to Tackle Facioscapulohumeral Muscular Dystrophy.

Authors:  Virginie Mariot; Julie Dumonceaux
Journal:  Front Genome Ed       Date:  2022-07-15
  2 in total

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