Literature DB >> 34309696

Brain structural changes in patients with cardio-facio-cutaneous syndrome: effects of BRAF gene mutation and epilepsy on brain development. A case-control study by quantitative magnetic resonance imaging.

Rosalinda Calandrelli1, Fabio Pilato2, Marco Panfili1, Domenica Battaglia3,4, Maria Luigia Gambardella3, Cesare Colosimo1,5.   

Abstract

PURPOSE: To evaluate the brain volumetric changes caused by BRAF gene mutation in non-epileptic CFC patients and the influence of the age of epilepsy onset on brain development in 2 cohorts of epileptic CFC patients.
METHODS: We enrolled CFC patients carrying BRAF gene mutations without epilepsy (4 patients) and with epilepsy (16 patients). CFC epileptic patients were divided into two cohorts based on the age of seizure onset: early-age onset (7 children) and late-age onset (9 adolescents). All three cohorts of patients underwent 3D FSPGR T1-weighted imaging to assess supratentorial and infratentorial brain volumes. Moreover, for each compartment, gray matter (GM), white matter (WM), and cerebrospinal fluid (CSF) volumes were measured. All measurements were compared with those of age-matched controls without neuroimaging abnormalities.
RESULTS: All CFC patients showed supratentorial and infratentorial WM reduction and supratentorial ventricular enlargement (p < 0.01). However, patients with early age of epilepsy onset, compared with the other two cohorts of CFC patients, showed both GM and a more pronounced WM volume reduction (p < 0.01).
CONCLUSION: In non-epileptic CFC children, we demonstrated WM volumetric reduction suggesting a direct effect of BRAF gene mutation on brain development. Nevertheless, in CFC epileptic patients, the age of epilepsy onset may contribute to brain atrophy. Brain atrophy in CFC patients, in part due to the natural history of the disease, may be worsened by epilepsy when it begins in the early ages because of interference with brain growth at that critical age of development.
© 2021. The Author(s), under exclusive licence to Springer-Verlag GmbH Germany, part of Springer Nature.

Entities:  

Keywords:  Brain atrophy; Cardio-facio-cutaneous syndrome; Epilepsy onset; High-resolution magnetic resonance imaging

Mesh:

Substances:

Year:  2021        PMID: 34309696     DOI: 10.1007/s00234-021-02769-w

Source DB:  PubMed          Journal:  Neuroradiology        ISSN: 0028-3940            Impact factor:   2.804


  40 in total

1.  Germline mutations in genes within the MAPK pathway cause cardio-facio-cutaneous syndrome.

Authors:  Pablo Rodriguez-Viciana; Osamu Tetsu; William E Tidyman; Anne L Estep; Brenda A Conger; Molly Santa Cruz; Frank McCormick; Katherine A Rauen
Journal:  Science       Date:  2006-01-26       Impact factor: 47.728

Review 2.  Perinatal features of the RASopathies: Noonan syndrome, cardiofaciocutaneous syndrome and Costello syndrome.

Authors:  Angela Myers; Jonathan A Bernstein; Marie-Luise Brennan; Cynthia Curry; Edward D Esplin; Jamie Fisher; Margaret Homeyer; Melanie A Manning; Eric A Muller; Anna-Kaisa Niemi; Laurie H Seaver; Susan R Hintz; Louanne Hudgins
Journal:  Am J Med Genet A       Date:  2014-09-22       Impact factor: 2.802

Review 3.  Cardio-facio-cutaneous syndrome: clinical features, diagnosis, and management guidelines.

Authors:  Mary Ella M Pierpont; Pilar L Magoulas; Saleh Adi; Maria Ines Kavamura; Giovanni Neri; Jacqueline Noonan; Elizabeth I Pierpont; Kent Reinker; Amy E Roberts; Suma Shankar; Joseph Sullivan; Melinda Wolford; Brenda Conger; Molly Santa Cruz; Katherine A Rauen
Journal:  Pediatrics       Date:  2014-09-01       Impact factor: 7.124

Review 4.  Epilepsy in RAS/MAPK syndrome: two cases of cardio-facio-cutaneous syndrome with epileptic encephalopathy and a literature review.

Authors:  Masao Adachi; Yu Abe; Yoko Aoki; Yoichi Matsubara
Journal:  Seizure       Date:  2011-08-25       Impact factor: 3.184

5.  A girl with Cardio-facio-cutaneous syndrome complicated with status epilepticus and acute encephalopathy.

Authors:  Keisuke Wakusawa; Satoru Kobayashi; Yu Abe; Soichiro Tanaka; Wakaba Endo; Takehiko Inui; Mitsutosi Iwaki; Shuei Watanabe; Noriko Togashi; Takahiro Nara; Tetsuya Niihori; Yoko Aoki; Kazuhiro Haginoya
Journal:  Brain Dev       Date:  2013-01-20       Impact factor: 1.961

6.  Neurological complications of cardio-facio-cutaneous syndrome.

Authors:  Grace Yoon; Jodine Rosenberg; Susan Blaser; Katherine A Rauen
Journal:  Dev Med Child Neurol       Date:  2007-12       Impact factor: 5.449

7.  Germline KRAS and BRAF mutations in cardio-facio-cutaneous syndrome.

Authors:  Tetsuya Niihori; Yoko Aoki; Yoko Narumi; Giovanni Neri; Hélène Cavé; Alain Verloes; Nobuhiko Okamoto; Raoul C M Hennekam; Gabriele Gillessen-Kaesbach; Dagmar Wieczorek; Maria Ines Kavamura; Kenji Kurosawa; Hirofumi Ohashi; Louise Wilson; Delphine Heron; Dominique Bonneau; Giuseppina Corona; Tadashi Kaname; Kenji Naritomi; Clarisse Baumann; Naomichi Matsumoto; Kumi Kato; Shigeo Kure; Yoichi Matsubara
Journal:  Nat Genet       Date:  2006-02-12       Impact factor: 38.330

8.  Clinical Report: Cognitive decline in a patient with Cardiofaciocutaneous syndrome.

Authors:  Sergio Cabrera; Chantal Morel; Maria Carmela Tartaglia
Journal:  Am J Med Genet A       Date:  2016-02-03       Impact factor: 2.802

Review 9.  The RASopathies: developmental syndromes of Ras/MAPK pathway dysregulation.

Authors:  William E Tidyman; Katherine A Rauen
Journal:  Curr Opin Genet Dev       Date:  2009-05-19       Impact factor: 5.578

Review 10.  A review of craniofacial and dental findings of the RASopathies.

Authors:  H Cao; N Alrejaye; O D Klein; A F Goodwin; S Oberoi
Journal:  Orthod Craniofac Res       Date:  2017-06       Impact factor: 1.826

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