Literature DB >> 34285418

Therapeutic base editing in the adult liver.

Coen C Paulusma1, Piter J Bosma2.   

Abstract

Year:  2021        PMID: 34285418     DOI: 10.1038/s41575-021-00491-9

Source DB:  PubMed          Journal:  Nat Rev Gastroenterol Hepatol        ISSN: 1759-5045            Impact factor:   46.802


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  2 in total

1.  In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels.

Authors:  Tanja Rothgangl; Melissa K Dennis; Paulo J C Lin; Rurika Oka; Dominik Witzigmann; Lukas Villiger; Weihong Qi; Martina Hruzova; Lucas Kissling; Daniela Lenggenhager; Costanza Borrelli; Sabina Egli; Nina Frey; Noëlle Bakker; John A Walker; Anastasia P Kadina; Denis V Victorov; Martin Pacesa; Susanne Kreutzer; Zacharias Kontarakis; Andreas Moor; Martin Jinek; Drew Weissman; Markus Stoffel; Ruben van Boxtel; Kevin Holden; Norbert Pardi; Beat Thöny; Johannes Häberle; Ying K Tam; Sean C Semple; Gerald Schwank
Journal:  Nat Biotechnol       Date:  2021-05-19       Impact factor: 54.908

2.  Moving somatic gene editing to the clinic: routes to market access and reimbursement in Europe.

Authors:  Tessel Rigter; David Klein; Stephanie S Weinreich; Martina C Cornel
Journal:  Eur J Hum Genet       Date:  2021-04-14       Impact factor: 4.246

  2 in total

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