Literature DB >> 34245199

Nusinersen improved respiratory function in spinal muscular atrophy type 2.

Ryuta Tanaka1,2, Fujiko Fukushima1, Keiichi Motoyama1, Chie Kobayashi1,2, Isho Izumi1.   

Abstract

Entities:  

Keywords:  Nusinersen; noninvasive ventilation; respiratory function tests; respiratory insufficiency; spinal muscular atrophies of childhood

Year:  2021        PMID: 34245199     DOI: 10.1111/ped.14510

Source DB:  PubMed          Journal:  Pediatr Int        ISSN: 1328-8067            Impact factor:   1.524


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  1 in total

Review 1.  Changes in Ventilatory Support Requirements of Spinal Muscular Atrophy (SMA) Patients Post Gene-Based Therapies.

Authors:  Panagiota Panagiotou; Christina Kanaka-Gantenbein; Athanasios G Kaditis
Journal:  Children (Basel)       Date:  2022-08-11
  1 in total

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