Literature DB >> 34116031

Endoscopic Ultrasound-guided Fine-needle Biopsy With or Without Rapid On-site Evaluation for Diagnosis of Solid Pancreatic Lesions: A Randomized Controlled Non-Inferiority Trial.

Stefano Francesco Crinò1, Roberto Di Mitri2, Nam Q Nguyen3, Ilaria Tarantino4, Germana de Nucci5, Pierre H Deprez6, Silvia Carrara7, Masayuki Kitano8, Vanessa M Shami9, Gloria Fernández-Esparrach10, Jan-Werner Poley11, Francisco Baldaque-Silva12, Takao Itoi13, Erminia Manfrin14, Laura Bernardoni15, Armando Gabbrielli15, Elisabetta Conte2, Elettra Unti16, Jeevinesh Naidu3, Andrew Ruszkiewicz17, Michele Amata4, Rosa Liotta18, Gianpiero Manes5, Franca Di Nuovo19, Ivan Borbath6, Mina Komuta20, Laura Lamonaca7, Daoud Rahal21, Keiichi Hatamaru8, Masahiro Itonaga8, Gianenrico Rizzatti22, Guido Costamagna23, Frediano Inzani24, Mariangela Curatolo24, Daniel S Strand9, Andrew Y Wang9, Àngels Ginès10, Oriol Sendino10, Marianna Signoretti25, Lydi M J W van Driel11, Karoly Dolapcsiev26, Yukitoshi Matsunami13, Schalk van der Merwe27, Hannah van Malenstein27, Francesca Locatelli28, Loredana Correale15, Aldo Scarpa29, Alberto Larghi23.   

Abstract

BACKGROUND AND AIMS: The benefit of rapid on-site evaluation (ROSE) on the diagnostic accuracy of endoscopic ultrasound-guided fine-needle biopsy (EUS-FNB) has never been evaluated in a randomized study. This trial aimed to test the hypothesis that in solid pancreatic lesions (SPLs), diagnostic accuracy of EUS-FNB without ROSE was not inferior to that of EUS-FNB with ROSE.
METHODS: A noninferiority study (noninferiority margin, 5%) was conducted at 14 centers in 8 countries. Patients with SPLs requiring tissue sampling were randomly assigned (1:1) to undergo EUS-FNB with or without ROSE using new-generation FNB needles. The touch-imprint cytology technique was used to perform ROSE. The primary endpoint was diagnostic accuracy, and secondary endpoints were safety, tissue core procurement, specimen quality, and sampling procedural time.
RESULTS: Eight hundred patients were randomized over an 18-month period, and 771 were analyzed (385 with ROSE and 386 without). Comparable diagnostic accuracies were obtained in both arms (96.4% with ROSE and 97.4% without ROSE, P = .396). Noninferiority of EUS-FNB without ROSE was confirmed with an absolute risk difference of 1.0% (1-sided 90% confidence interval, -1.1% to 3.1%; noninferiority P < .001). Safety and sample quality of histologic specimens were similar in both groups. A significantly higher tissue core rate was obtained by EUS-FNB without ROSE (70.7% vs. 78.0%, P = .021), with a significantly shorter mean sampling procedural time (17.9 ± 8.8 vs 11.7 ± 6.0 minutes, P < .0001).
CONCLUSIONS: EUS-FNB demonstrated high diagnostic accuracy in evaluating SPLs independently on execution of ROSE. When new-generation FNB needles are used, ROSE should not be routinely recommended. (ClinicalTrial.gov number NCT03322592.).
Copyright © 2021 AGA Institute. Published by Elsevier Inc. All rights reserved.

Entities:  

Keywords:  Diagnostic Accuracy; Endoscopic Ultrasound Tissue Acquisition; Pancreatic Cancer; Preoperative Sampling

Mesh:

Year:  2021        PMID: 34116031     DOI: 10.1053/j.gastro.2021.06.005

Source DB:  PubMed          Journal:  Gastroenterology        ISSN: 0016-5085            Impact factor:   22.682


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