Literature DB >> 33859432

Gene therapy needs a long-term approach.

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Abstract

Year:  2021        PMID: 33859432     DOI: 10.1038/s41591-021-01333-6

Source DB:  PubMed          Journal:  Nat Med        ISSN: 1078-8956            Impact factor:   53.440


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  4 in total

Review 1.  Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies.

Authors:  Carsten W Lederer; Lola Koniali; Tina Buerki-Thurnherr; Panayiota L Papasavva; Stefania La Grutta; Amelia Licari; Frantisek Staud; Donato Bonifazi; Marina Kleanthous
Journal:  Pharmaceutics       Date:  2022-04-05       Impact factor: 6.525

2.  Generation and analysis of innovative genomically humanized knockin SOD1, TARDBP (TDP-43), and FUS mouse models.

Authors:  Anny Devoy; Georgia Price; Francesca De Giorgio; Rosie Bunton-Stasyshyn; David Thompson; Samanta Gasco; Alasdair Allan; Gemma F Codner; Remya R Nair; Charlotte Tibbit; Ross McLeod; Zeinab Ali; Judith Noda; Alessandro Marrero-Gagliardi; José M Brito-Armas; Chloe Williams; Muhammet M Öztürk; Michelle Simon; Edward O'Neill; Sam Bryce-Smith; Jackie Harrison; Gemma Atkins; Silvia Corrochano; Michelle Stewart; Jonathan D Gilthorpe; Lydia Teboul; Abraham Acevedo-Arozena; Elizabeth M C Fisher; Thomas J Cunningham
Journal:  iScience       Date:  2021-11-15

Review 3.  It's Getting Complicated-A Fresh Look at p53-MDM2-ARF Triangle in Tumorigenesis and Cancer Therapy.

Authors:  Che-Pei Kung; Jason D Weber
Journal:  Front Cell Dev Biol       Date:  2022-01-26

4.  Self-Repairing Herpesvirus Saimiri Deletion Variants.

Authors:  Ines Heyn; Linda Bremer; Philipp Zingler; Helmut Fickenscher
Journal:  Viruses       Date:  2022-07-13       Impact factor: 5.818

  4 in total

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