Literature DB >> 33679746

Somatic Mutations and the Risk of Undifferentiated Autoinflammatory Disease in MDS: An Under-Recognized but Prognostically Important Complication.

Abdulla Watad1,2, Mark Kacar1,3, Nicola Luigi Bragazzi4, Qiao Zhou1,5, Miriam Jassam3, Jan Taylor6, Eve Roman7, Alexandra Smith7, Richard A Jones8, Howard Amital2, Catherine Cargo8, Dennis McGonagle1, Sinisa Savic1,3.   

Abstract

Objectives: We theorized that myelodysplastic syndrome (MDS) with somatic mutations and karyotype abnormalities are associated with autoinflammation, and that the presence of autoinflammatory disease affected prognosis in MDS.
Methods: One hundred thirty-four MDS patients were assessed for the prevalence of autoinflammatory complications and its link with karyotypes and somatic mutation status. Autoinflammatory complications were described either as well-defined autoinflammatory diseases (AD) or undifferentiated "autoinflammatory disease" (UAD) (defined as CRP over 10.0 mg/L on five consecutive occasions, taken at separate times and not explained by infection). Several patient characteristics including demographic, clinical, laboratory, cytogenetics charts, and outcomes, were compared between different groups.
Results: Sixty-two (46.3%) patients had an autoinflammatory complication manifesting as arthralgia (43.5% vs. 23.6%, p = 0.0146), arthritis (30.6% vs. 15.3%, p = 0.0340), skin rash (27.4% vs. 12.5%, p = 0.0301), pleuritis (14.5% vs. 4.2%, p = 0.0371) and unexplained fever (27.4% vs. 0%, p < 0.0001). AD were found in 7.4% of MDS patients (with polymyalgia rheumatic being the most frequently one). Classical autoimmune diseases were found only in 4 MDS patients (3.0%). Transcription factor pathway mutations (RUNX1, BCOR, WTI, TP53) (OR 2.20 [95%CI 1.02-4.75], p = 0.0451) and abnormal karyotypes (OR 2.76 [95%CI 1.22-6.26], p = 0.0153) were associated with autoinflammatory complications. Acute leukaemic transformation was more frequent in MDS patients with autoinflammatory features than those without (27.4% vs. 9.7%, p = 0.0080). Conclusions: Autoinflammatory complications are common in MDS. Somatic mutations of transcription factor pathways and abnormal karyotypes are associated with greater risk of autoinflammatory complications, which are themselves linked to malignant transformation and a worse prognosis.
Copyright © 2021 Watad, Kacar, Bragazzi, Zhou, Jassam, Taylor, Roman, Smith, Jones, Amital, Cargo, McGonagle and Savic.

Entities:  

Keywords:  autoinflammation; molecular characterization; myelodysplatic syndrome; somatic mutations; undifferentiated autoinflammatory disease

Mesh:

Substances:

Year:  2021        PMID: 33679746      PMCID: PMC7933213          DOI: 10.3389/fimmu.2021.610019

Source DB:  PubMed          Journal:  Front Immunol        ISSN: 1664-3224            Impact factor:   7.561


  47 in total

Review 1.  Molecular mechanisms regulating NLRP3 inflammasome activation.

Authors:  Eun-Kyeong Jo; Jin Kyung Kim; Dong-Min Shin; Chihiro Sasakawa
Journal:  Cell Mol Immunol       Date:  2015-11-09       Impact factor: 11.530

Review 2.  Autoimmunity, Clonal Hematopoiesis, and Myeloid Neoplasms.

Authors:  Delamo I Bekele; Mrinal M Patnaik
Journal:  Rheum Dis Clin North Am       Date:  2020-06-10       Impact factor: 2.670

3.  Activating CBL mutations are associated with a distinct MDS/MPN phenotype.

Authors:  Juliana Schwaab; Thomas Ernst; Philipp Erben; Jenny Rinke; Susanne Schnittger; Philipp Ströbel; Georgia Metzgeroth; Max Mossner; Torsten Haferlach; Nicholas C P Cross; Andreas Hochhaus; Wolf-Karsten Hofmann; Andreas Reiter
Journal:  Ann Hematol       Date:  2012-08-10       Impact factor: 3.673

Review 4.  The genetics of myelodysplastic syndrome: from clonal haematopoiesis to secondary leukaemia.

Authors:  Adam S Sperling; Christopher J Gibson; Benjamin L Ebert
Journal:  Nat Rev Cancer       Date:  2016-11-11       Impact factor: 60.716

5.  Tumor suppressor p53 inhibits autoimmune inflammation and macrophage function.

Authors:  Shi-Jun Zheng; Salah-Eddine Lamhamedi-Cherradi; Pu Wang; Lingyun Xu; Youhai H Chen
Journal:  Diabetes       Date:  2005-05       Impact factor: 9.461

Review 6.  Autoimmunity and hematologic malignancies: associations and mechanisms.

Authors:  Damali N Martin; Isis S Mikhail; Ola Landgren
Journal:  Leuk Lymphoma       Date:  2009-04

7.  Giant Cell Arteritis: From Pathogenesis to Therapeutic Management.

Authors:  Ryu Watanabe; Jörg J Goronzy; Gerald Berry; Y Joyce Liao; Cornelia M Weyand
Journal:  Curr Treatm Opt Rheumatol       Date:  2016-04-11

8.  Bone progenitor dysfunction induces myelodysplasia and secondary leukaemia.

Authors:  Marc H G P Raaijmakers; Siddhartha Mukherjee; Shangqin Guo; Siyi Zhang; Tatsuya Kobayashi; Jesse A Schoonmaker; Benjamin L Ebert; Fatima Al-Shahrour; Robert P Hasserjian; Edward O Scadden; Zinmar Aung; Marc Matza; Matthias Merkenschlager; Charles Lin; Johanna M Rommens; David T Scadden
Journal:  Nature       Date:  2010-03-21       Impact factor: 49.962

9.  Clonal hematopoiesis in patients with rheumatoid arthritis.

Authors:  Paula Savola; Sofie Lundgren; Mikko A I Keränen; Henrikki Almusa; Pekka Ellonen; Marjatta Leirisalo-Repo; Tiina Kelkka; Satu Mustjoki
Journal:  Blood Cancer J       Date:  2018-07-26       Impact factor: 11.037

Review 10.  Unraveling the Pathogenesis of MDS: The NLRP3 Inflammasome and Pyroptosis Drive the MDS Phenotype.

Authors:  David A Sallman; Thomas Cluzeau; Ashley A Basiorka; Alan List
Journal:  Front Oncol       Date:  2016-06-16       Impact factor: 6.244

View more
  4 in total

Review 1.  Inflammatory Cytokines Shape an Altered Immune Response During Myeloid Malignancies.

Authors:  Virginia Camacho; Valeriya Kuznetsova; Robert S Welner
Journal:  Front Immunol       Date:  2021-11-03       Impact factor: 7.561

2.  Case Report: Genetic Double Strike: VEXAS and TET2-Positive Myelodysplastic Syndrome in a Patient With Long-Standing Refractory Autoinflammatory Disease.

Authors:  Fabian Lötscher; Luca Seitz; Helena Simeunovic; Adela-Cristina Sarbu; Naomi A Porret; Laurence Feldmeyer; Luca Borradori; Nicolas Bonadies; Britta Maurer
Journal:  Front Immunol       Date:  2022-01-20       Impact factor: 7.561

Review 3.  Improving Diagnosis and Clinical Management of Acquired Systemic Autoinflammatory Diseases.

Authors:  Adam Al-Hakim; Anoop Mistry; Sinisa Savic
Journal:  J Inflamm Res       Date:  2022-10-10

4.  Novel somatic mutations in UBA1 as a cause of VEXAS syndrome.

Authors:  James A Poulter; Jason C Collins; Catherine Cargo; Ruth M De Tute; Paul Evans; Daniela Ospina Cardona; David T Bowen; Joanna R Cunnington; Elaine Baguley; Mark Quinn; Michael Green; Dennis McGonagle; David B Beck; Achim Werner; Sinisa Savic
Journal:  Blood       Date:  2021-07-01       Impact factor: 25.476

  4 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.