Literature DB >> 33648526

Correction to: Long-term survival with sebelipase alfa enzyme replacement therapy in infants with rapidly progressive lysosomal acid lipase deficiency: final results from 2 open-label studies.

Suresh Vijay1, Anais Brassier2, Arunabha Ghosh3, Simona Fecarotta4, Florian Abel5, Sachin Marulkar5, Simon A Jones3.   

Abstract

Entities:  

Year:  2021        PMID： 33648526      PMCID： PMC7923548          DOI： 10.1186/s13023-021-01753-0

Source DB:  PubMed          Journal:  Orphanet J Rare Dis        ISSN： 1750-1172            Impact factor:   4.123


× No keyword cloud information.
  1 in total

1.  Long-term survival with sebelipase alfa enzyme replacement therapy in infants with rapidly progressive lysosomal acid lipase deficiency: final results from 2 open-label studies.

Authors:  Suresh Vijay; Anais Brassier; Arunabha Ghosh; Simona Fecarotta; Florian Abel; Sachin Marulkar; Simon A Jones
Journal:  Orphanet J Rare Dis       Date:  2021-01-06       Impact factor: 4.123
  1 in total
  1 in total

1.  Lessons Learned From the Long-Term Use of Enzyme Replacement Therapy in the Treatment of Lysosomal Acid Lipase Deficiency.

Authors:  Alanna Strong; Can Ficicioglu
Journal:  J Pediatr Gastroenterol Nutr       Date:  2022-05-17       Impact factor: 3.288
  1 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.