Literature DB >> 33604967

Minimal detectable change and minimal clinically important difference in spinal muscular atrophy patients.

Juan F Vázquez-Costa1,2,3,4, David Hervás5.   

Abstract

Entities:  

Year:  2021        PMID: 33604967     DOI: 10.1111/ene.14780

Source DB:  PubMed          Journal:  Eur J Neurol        ISSN: 1351-5101            Impact factor:   6.089


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  2 in total

1.  Nusinersen in Adults with 5q Spinal Muscular Atrophy: a Systematic Review and Meta-analysis.

Authors:  Maria Gavriilaki; Maria Moschou; Vasileios Papaliagkas; Konstantinos Notas; Evangelia Chatzikyriakou; Sotirios Papagiannopoulos; Marianthi Arnaoutoglou; Vasilios K Kimiskidis
Journal:  Neurotherapeutics       Date:  2022-02-17       Impact factor: 6.088

2.  A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data.

Authors:  Tina Duong; Hannah Staunton; Jessica Braid; Aurelie Barriere; Ben Trzaskoma; Ling Gao; Tom Willgoss; Rosangel Cruz; Nicole Gusset; Ksenija Gorni; Sharan Randhawa; Lida Yang; Carole Vuillerot
Journal:  Front Neurol       Date:  2022-01-17       Impact factor: 4.003

  2 in total

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