| Literature DB >> 33398081 |
Yoel Hirsch1, Chayada Tangshewinsirikul2,3, Kevin T Booth4,5, Hela Azaiez4, Devorah Yefet6, Adina Quint6, Tzvi Weiden6, Zippora Brownstein7, Michal Macarov8, Bella Davidov9, John Pappas10, Rachel Rabin10, Margaret A Kenna11,12, Andrea M Oza11,13, Katherine Lafferty13,14, Sami S Amr12,13,15, Heidi L Rehm12,13,15,16,17, Diana L Kolbe4, Kathy Frees4, Carla Nishimura4, Minjie Luo18, Chantal Farra19, Cynthia C Morton3,12,15,17,20, Sholem Y Scher1, Josef Ekstein1, Karen B Avraham21, Richard J H Smith22, Jun Shen23,24,25.
Abstract
Nonsyndromic hearing loss is genetically heterogeneous. Despite comprehensive genetic testing, many cases remain unsolved because the clinical significance of identified variants is uncertain or because biallelic pathogenic variants are not identified for presumed autosomal recessive cases. Common synonymous variants are often disregarded. Determining the pathogenicity of synonymous variants may improve genetic diagnosis. We report a synonymous variant c.9861 C > T/p.(Gly3287=) in MYO15A in homozygosity or compound heterozygosity with another pathogenic or likely pathogenic MYO15A variant in 10 unrelated families with nonsyndromic sensorineural hearing loss. Biallelic variants in MYO15A were identified in 21 affected and were absent in 22 unaffected siblings. A mini-gene assay confirms that the synonymous variant leads to abnormal splicing. The variant is enriched in the Ashkenazi Jewish population. Individuals carrying biallelic variants involving c.9861 C > T often exhibit progressive post-lingual hearing loss distinct from the congenital profound deafness typically associated with biallelic loss-of-function MYO15A variants. This study establishes the pathogenicity of the c.9861 C > T variant in MYO15A and expands the phenotypic spectrum of MYO15A-related hearing loss. Our work also highlights the importance of multicenter collaboration and data sharing to establish the pathogenicity of a relatively common synonymous variant for improved diagnosis and management of hearing loss.Entities:
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Year: 2021 PMID: 33398081 PMCID: PMC8187401 DOI: 10.1038/s41431-020-00790-w
Source DB: PubMed Journal: Eur J Hum Genet ISSN: 1018-4813 Impact factor: 5.351