Literature DB >> 33387903

Hemimegalencephaly and tuberous sclerosis complex: A rare yet challenging association.

Christina Sidira1, Efthymia Vargiami1, Pinelopi Dragoumi1, Dimitrios I Zafeiriou2.   

Abstract

Hemimegalencephaly is a rare malformation of cortical development characterised by enlargement of one cerebral hemisphere. The association between hemimegalencephaly and tuberous sclerosis complex, an autosomal dominant genetic disorder, is uncommon and has so far been reported only in a few cases. Intractable epilepsy and severe developmental delay are typical clinical manifestations. Aberrant activation of the mTOR signalling pathway is considered to be the hallmark of the pathogenesis of these two disorders. Thus, mTOR inhibitors such as everolimus represent a promising therapeutic approach to mTOR-associated manifestations. We present a thorough literature review of the association between hemimegaloencephaly and tuberous sclerosis complex.
Copyright © 2020 European Paediatric Neurology Society. Published by Elsevier Ltd. All rights reserved.

Entities:  

Keywords:  Everolimus; Hemimegalencephaly; Malformations of cortical development; Tuberous sclerosis complex; mTOR inhibitors

Mesh:

Substances:

Year:  2020        PMID: 33387903     DOI: 10.1016/j.ejpn.2020.12.007

Source DB:  PubMed          Journal:  Eur J Paediatr Neurol        ISSN: 1090-3798            Impact factor:   3.140


  1 in total

1.  Hemimegalencephaly: A rare congenital malformation of cortical development.

Authors:  Vikash Jaiswal; Muhammad Hanif; Zouina Sarfraz; Gaurav Nepal; Sidra Naz; Dattatreya Mukherjee; Samir Ruxmohan
Journal:  Clin Case Rep       Date:  2021-12-18
  1 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.