Literature DB >> 33353801

A Decision for Life - Treatment decisions in newly diagnosed families with spinal muscular atrophy (SMA).

Nicole Gusset1, Yasemin Erbas2, Olga Germanenko3, Kacper Rucinski4, Eva Stumpe5, Mencía de Lemus6.   

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Year:  2020        PMID: 33353801     DOI: 10.1016/j.ejpn.2020.11.003

Source DB:  PubMed          Journal:  Eur J Paediatr Neurol        ISSN: 1090-3798            Impact factor:   3.140


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  2 in total

1.  Systematic Literature Review to Assess the Cost and Resource Use Associated with Spinal Muscular Atrophy Management.

Authors:  Noman Paracha; Pollyanna Hudson; Stephen Mitchell; C Simone Sutherland
Journal:  Pharmacoeconomics       Date:  2021-11-11       Impact factor: 4.981

2.  Therapeutic Decision-Making Under Uncertainty in the Management of Spinal Muscular Atrophy: Results From DECISIONS-SMA Study.

Authors:  Gustavo Saposnik; Ana Camacho; Paola Díaz-Abós; María Brañas-Pampillón; Victoria Sánchez-Menéndez; Rosana Cabello-Moruno; María Terzaghi; Jorge Maurino; Ignacio Málaga
Journal:  Neurol Ther       Date:  2022-06-03
  2 in total

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