Literature DB >> 33211935

Sourcing Photoreceptor-like Cells for Treating Vision Loss.

Rajendra S Apte1.   

Abstract

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Year:  2020        PMID: 33211935      PMCID: PMC9369200          DOI: 10.1056/NEJMcibr2027602

Source DB:  PubMed          Journal:  N Engl J Med        ISSN: 0028-4793            Impact factor:   176.079


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  5 in total

1.  Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.

Authors:  Stephen Russell; Jean Bennett; Jennifer A Wellman; Daniel C Chung; Zi-Fan Yu; Amy Tillman; Janet Wittes; Julie Pappas; Okan Elci; Sarah McCague; Dominique Cross; Kathleen A Marshall; Jean Walshire; Taylor L Kehoe; Hannah Reichert; Maria Davis; Leslie Raffini; Lindsey A George; F Parker Hudson; Laura Dingfield; Xiaosong Zhu; Julia A Haller; Elliott H Sohn; Vinit B Mahajan; Wanda Pfeifer; Michelle Weckmann; Chris Johnson; Dina Gewaily; Arlene Drack; Edwin Stone; Katie Wachtel; Francesca Simonelli; Bart P Leroy; J Fraser Wright; Katherine A High; Albert M Maguire
Journal:  Lancet       Date:  2017-07-14       Impact factor: 79.321

2.  Human embryonic stem cell-derived retinal pigment epithelium in patients with age-related macular degeneration and Stargardt's macular dystrophy: follow-up of two open-label phase 1/2 studies.

Authors:  Steven D Schwartz; Carl D Regillo; Byron L Lam; Dean Eliott; Philip J Rosenfeld; Ninel Z Gregori; Jean-Pierre Hubschman; Janet L Davis; Gad Heilwell; Marc Spirn; Joseph Maguire; Roger Gay; Jane Bateman; Rosaleen M Ostrick; Debra Morris; Matthew Vincent; Eddy Anglade; Lucian V Del Priore; Robert Lanza
Journal:  Lancet       Date:  2014-10-15       Impact factor: 79.321

Review 3.  NAD+ and sirtuins in retinal degenerative diseases: A look at future therapies.

Authors:  Jonathan B Lin; Rajendra S Apte
Journal:  Prog Retin Eye Res       Date:  2018-06-12       Impact factor: 21.198

Review 4.  STEM CELL THERAPIES, GENE-BASED THERAPIES, OPTOGENETICS, AND RETINAL PROSTHETICS: Current State and Implications for the Future.

Authors:  Edward H Wood; Peter H Tang; Irina De la Huerta; Edward Korot; Stephanie Muscat; Daniel A Palanker; George A Williams
Journal:  Retina       Date:  2019-05       Impact factor: 4.256

5.  Pharmacologic fibroblast reprogramming into photoreceptors restores vision.

Authors:  Koray Dogan Kaya; Yan Fan; Biraj Mahato; Nathalie Sumien; Ritu A Shetty; Wei Zhang; Delaney Davis; Thomas Mock; Subrata Batabyal; Aiguo Ni; Samarendra Mohanty; Zongchao Han; Rafal Farjo; Michael J Forster; Anand Swaroop; Sai H Chavala
Journal:  Nature       Date:  2020-04-15       Impact factor: 49.962

  5 in total

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