Literature DB >> 33176091

Givosiran for Acute Intermittent Porphyria.

Elena Gomá-Garcés1, M Vanessa Pérez-Gómez1, Alberto Ortíz1.   

Abstract

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Year:  2020        PMID: 33176091     DOI: 10.1056/NEJMc2026458

Source DB:  PubMed          Journal:  N Engl J Med        ISSN: 0028-4793            Impact factor:   91.245


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  6 in total

1.  Endothelial Dysfunction in Acute Hepatic Porphyrias.

Authors:  Andrea Ricci; Gilda Sandri; Matteo Marcacci; Elena Di Pierro; Francesca Granata; Chiara Cuoghi; Stefano Marchini; Antonello Pietrangelo; Paolo Ventura
Journal:  Diagnostics (Basel)       Date:  2022-05-24

2.  Severe homocysteinemia in two givosiran-treated porphyria patients: is free heme deficiency the culprit?

Authors:  Petro E Petrides; Michael Klein; Elfriede Schuhmann; Heike Torkler; Brigitte Molitor; Christian Loehr; Zahra Obermeier; Maria K Beykirch
Journal:  Ann Hematol       Date:  2021-05-29       Impact factor: 3.673

3.  Keeping up with the COVID's-Could siRNA-based antivirals be a part of the answer?

Authors:  Helen Forgham; Aleksandr Kakinen; Ruirui Qiao; Thomas P Davis
Journal:  Exploration (Beijing)       Date:  2022-07-14

Review 4.  Directing the Way-Receptor and Chemical Targeting Strategies for Nucleic Acid Delivery.

Authors:  Ricarda Carolin Steffens; Ernst Wagner
Journal:  Pharm Res       Date:  2022-09-15       Impact factor: 4.580

5.  Renal Function Decline With Small Interfering RNA Silencing Aminolevulinic Acid Synthase 1 (ALAS1).

Authors:  Hélène Lazareth; Antoine Poli; Yohan Bignon; Arienne Mirmiran; Marion Rabant; Raphaël Cohen; Caroline Schmitt; Hervé Puy; Alexandre Karras; Laurent Gouya; Nicolas Pallet
Journal:  Kidney Int Rep       Date:  2021-04-15

Review 6.  Kidney Involvement in Acute Hepatic Porphyrias: Pathophysiology and Diagnostic Implications.

Authors:  Andrea Ricci; Claudio Carmine Guida; Paola Manzini; Chiara Cuoghi; Paolo Ventura
Journal:  Diagnostics (Basel)       Date:  2021-12-10
  6 in total

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