Elena Gomá-Garcés1, M Vanessa Pérez-Gómez1, Alberto Ortíz1. Show Affiliations » 1. Hospital Universitario Fundación Jiménez Díaz, Madrid, Spain elegomgarces@gmail.com.
Abstract
Mesh: See more » Acetylgalactosamine/analogs & derivativesAmidesHumansPorphyria, Acute Intermittent/diagnosisPyrrolidinesRNA InterferenceRNAi Therapeutics
Substances: See more » AmidesPyrrolidinesAcetylgalactosaminegivosiran
Year: 2020 PMID: 33176091 DOI: 10.1056/NEJMc2026458
Source DB: PubMed Journal: N Engl J Med ISSN: 0028-4793 Impact factor: 91.245