Literature DB >> 32949809

Successful SCID gene therapy in infant with disseminated BCG.

Gabriela Maron1, Sue Kaste2, Armita Bahrami3, Michael Neel4, Harry L Malech5, Jennifer M Puck6, Morton J Cowan6, Stephen Gottschalk7, Ewelina Mamcarz8.   

Abstract

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Year:  2020        PMID: 32949809      PMCID: PMC7870513          DOI: 10.1016/j.jaip.2020.09.004

Source DB:  PubMed          Journal:  J Allergy Clin Immunol Pract


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  8 in total

1.  Bacille Calmette-Guerin (BCG) complications in children with severe combined immunodeficiency (SCID).

Authors:  Galia Barkai; Raz Somech; Tali Stauber; Aviv Barziali; Shoshana Greenberger
Journal:  Infect Dis (Lond)       Date:  2019-06-17

2.  BCG vaccination in patients with severe combined immunodeficiency: complications, risks, and vaccination policies.

Authors:  Beatriz E Marciano; Chiung-Yu Huang; Gyan Joshi; Nima Rezaei; Beatriz Costa Carvalho; Zoe Allwood; Aydan Ikinciogullari; Shereen M Reda; Andrew Gennery; Vojtech Thon; Francisco Espinosa-Rosales; Waleed Al-Herz; Oscar Porras; Anna Shcherbina; Anna Szaflarska; Şebnem Kiliç; Jose L Franco; Andrea C Gómez Raccio; Persio Roxo; Isabel Esteves; Nermeen Galal; Anete Sevciovic Grumach; Salem Al-Tamemi; Alisan Yildiran; Julio C Orellana; Masafumi Yamada; Tomohiro Morio; Diana Liberatore; Yoshitoshi Ohtsuka; Yu-Lung Lau; Ryuta Nishikomori; Carlos Torres-Lozano; Juliana T L Mazzucchelli; Maria M S Vilela; Fabiola S Tavares; Luciana Cunha; Jorge A Pinto; Sara E Espinosa-Padilla; Leticia Hernandez-Nieto; Reem A Elfeky; Tadashi Ariga; Heike Toshio; Figen Dogu; Funda Cipe; Renata Formankova; M Enriqueta Nuñez-Nuñez; Liliana Bezrodnik; Jose Gonçalo Marques; María I Pereira; Viviana Listello; Mary A Slatter; Zohreh Nademi; Danuta Kowalczyk; Thomas A Fleisher; Graham Davies; Bénédicte Neven; Sergio D Rosenzweig
Journal:  J Allergy Clin Immunol       Date:  2014-04       Impact factor: 10.793

3.  SCID genotype and 6-month posttransplant CD4 count predict survival and immune recovery.

Authors:  Elie Haddad; Brent R Logan; Linda M Griffith; Rebecca H Buckley; Roberta E Parrott; Susan E Prockop; Trudy N Small; Jessica Chaisson; Christopher C Dvorak; Megan Murnane; Neena Kapoor; Hisham Abdel-Azim; Imelda C Hanson; Caridad Martinez; Jack J H Bleesing; Sharat Chandra; Angela R Smith; Matthew E Cavanaugh; Soma Jyonouchi; Kathleen E Sullivan; Lauri Burroughs; Suzanne Skoda-Smith; Ann E Haight; Audrey G Tumlin; Troy C Quigg; Candace Taylor; Blachy J Dávila Saldaña; Michael D Keller; Christine M Seroogy; Kenneth B Desantes; Aleksandra Petrovic; Jennifer W Leiding; David C Shyr; Hélène Decaluwe; Pierre Teira; Alfred P Gillio; Alan P Knutsen; Theodore B Moore; Morris Kletzel; John A Craddock; Victor Aquino; Jeffrey H Davis; Lolie C Yu; Geoffrey D E Cuvelier; Jeffrey J Bednarski; Frederick D Goldman; Elizabeth M Kang; Evan Shereck; Matthew H Porteus; James A Connelly; Thomas A Fleisher; Harry L Malech; William T Shearer; Paul Szabolcs; Monica S Thakar; Mark T Vander Lugt; Jennifer Heimall; Ziyan Yin; Michael A Pulsipher; Sung-Yun Pai; Donald B Kohn; Jennifer M Puck; Morton J Cowan; Richard J O'Reilly; Luigi D Notarangelo
Journal:  Blood       Date:  2018-08-28       Impact factor: 22.113

4.  Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1.

Authors:  Ewelina Mamcarz; Sheng Zhou; Timothy Lockey; Hossam Abdelsamed; Shane J Cross; Guolian Kang; Zhijun Ma; Jose Condori; Jola Dowdy; Brandon Triplett; Chen Li; Gabriela Maron; Juan C Aldave Becerra; Joseph A Church; Elif Dokmeci; James T Love; Ana C da Matta Ain; Hedi van der Watt; Xing Tang; William Janssen; Byoung Y Ryu; Suk See De Ravin; Mitchell J Weiss; Benjamin Youngblood; Janel R Long-Boyle; Stephen Gottschalk; Michael M Meagher; Harry L Malech; Jennifer M Puck; Morton J Cowan; Brian P Sorrentino
Journal:  N Engl J Med       Date:  2019-04-18       Impact factor: 91.245

5.  Successful treatment of disseminated BCG in a patient with severe combined immunodeficiency.

Authors:  Lauren L Smith; Benjamin L Wright; Rebecca H Buckley
Journal:  J Allergy Clin Immunol Pract       Date:  2015-01-22

6.  Transplantation outcomes for severe combined immunodeficiency, 2000-2009.

Authors:  Sung-Yun Pai; Brent R Logan; Linda M Griffith; Rebecca H Buckley; Roberta E Parrott; Christopher C Dvorak; Neena Kapoor; Imelda C Hanson; Alexandra H Filipovich; Soma Jyonouchi; Kathleen E Sullivan; Trudy N Small; Lauri Burroughs; Suzanne Skoda-Smith; Ann E Haight; Audrey Grizzle; Michael A Pulsipher; Ka Wah Chan; Ramsay L Fuleihan; Elie Haddad; Brett Loechelt; Victor M Aquino; Alfred Gillio; Jeffrey Davis; Alan Knutsen; Angela R Smith; Theodore B Moore; Marlis L Schroeder; Frederick D Goldman; James A Connelly; Matthew H Porteus; Qun Xiang; William T Shearer; Thomas A Fleisher; Donald B Kohn; Jennifer M Puck; Luigi D Notarangelo; Morton J Cowan; Richard J O'Reilly
Journal:  N Engl J Med       Date:  2014-07-31       Impact factor: 91.245

7.  A modified γ-retrovirus vector for X-linked severe combined immunodeficiency.

Authors:  Salima Hacein-Bey-Abina; Sung-Yun Pai; H Bobby Gaspar; Myriam Armant; Charles C Berry; Stephane Blanche; Jack Bleesing; Johanna Blondeau; Helen de Boer; Karen F Buckland; Laure Caccavelli; Guilhem Cros; Satiro De Oliveira; Karen S Fernández; Dongjing Guo; Chad E Harris; Gregory Hopkins; Leslie E Lehmann; Annick Lim; Wendy B London; Johannes C M van der Loo; Nirav Malani; Frances Male; Punam Malik; M Angélica Marinovic; Anne-Marie McNicol; Despina Moshous; Benedicte Neven; Matías Oleastro; Capucine Picard; Jerome Ritz; Christine Rivat; Axel Schambach; Kit L Shaw; Eric A Sherman; Leslie E Silberstein; Emmanuelle Six; Fabien Touzot; Alla Tsytsykova; Jinhua Xu-Bayford; Christopher Baum; Frederic D Bushman; Alain Fischer; Donald B Kohn; Alexandra H Filipovich; Luigi D Notarangelo; Marina Cavazzana; David A Williams; Adrian J Thrasher
Journal:  N Engl J Med       Date:  2014-10-09       Impact factor: 91.245

8.  Gene therapy for severe combined immunodeficiencies and beyond.

Authors:  Alain Fischer; Salima Hacein-Bey-Abina
Journal:  J Exp Med       Date:  2020-01-06       Impact factor: 14.307

  8 in total

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