Literature DB >> 32877590

Janus Kinase Inhibition in the Aicardi-Goutières Syndrome.

Adeline Vanderver1, Laura Adang1, Francesco Gavazzi1, Katherine McDonald1, Guy Helman2, David B Frank3, Nicole Jaffe3, Sabrina W Yum3, Abigail Collins4, Stephanie R Keller5, Pierre Lebon6, Jean-François Meritet7, Jullie Rhee8, Asako Takanohashi3, Thais Armangue9, Nicole Ulrick3, Omar Sherbini3, Jamie Koh3, Kyle Peer3, Constance Besnier3, Carly Scher3, Katherine Boyle3, Holly Dubbs3, Julia Kramer-Golinkoff3, Amy Pizzino3, Sarah Woidill3, Justine Shults10.   

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Year:  2020        PMID: 32877590      PMCID: PMC7495410          DOI: 10.1056/NEJMc2001362

Source DB:  PubMed          Journal:  N Engl J Med        ISSN: 0028-4793            Impact factor:   91.245


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  5 in total

1.  Aicardi goutières syndrome is associated with pulmonary hypertension.

Authors:  Laura A Adang; David B Frank; Ahmed Gilani; Asako Takanohashi; Nicole Ulrick; Abigail Collins; Zachary Cross; Csaba Galambos; Guy Helman; Usama Kanaan; Stephanie Keller; Dawn Simon; Omar Sherbini; Brian D Hanna; Adeline L Vanderver
Journal:  Mol Genet Metab       Date:  2018-09-07       Impact factor: 4.797

2.  Efficacy of JAK1/2 inhibition in the treatment of chilblain lupus due to TREX1 deficiency.

Authors:  Coralie Briand; Marie-Louise Frémond; Didier Bessis; Aurélia Carbasse; Gillian I Rice; Vincent Bondet; Darragh Duffy; Lucienne Chatenoud; Stéphane Blanche; Yanick J Crow; Bénédicte Neven
Journal:  Ann Rheum Dis       Date:  2018-10-03       Impact factor: 19.103

3.  An open-label trial of JAK 1/2 blockade in progressive IFIH1-associated neuroinflammation.

Authors:  Kavitha Kothur; Sushil Bandodkar; Stephanie Chu; Louise Wienholt; Alexandra Johnson; Peter Barclay; Paul A Brogan; Gillian I Rice; Yanick J Crow; Russell C Dale
Journal:  Neurology       Date:  2018-01-10       Impact factor: 9.910

4.  Clinical and molecular phenotype of Aicardi-Goutieres syndrome.

Authors:  Gillian Rice; Teresa Patrick; Rekha Parmar; Claire F Taylor; Alec Aeby; Jean Aicardi; Rafael Artuch; Simon Attard Montalto; Carlos A Bacino; Bruno Barroso; Peter Baxter; Willam S Benko; Carsten Bergmann; Enrico Bertini; Roberta Biancheri; Edward M Blair; Nenad Blau; David T Bonthron; Tracy Briggs; Louise A Brueton; Han G Brunner; Christopher J Burke; Ian M Carr; Daniel R Carvalho; Kate E Chandler; Hans-Jurgen Christen; Peter C Corry; Frances M Cowan; Helen Cox; Stefano D'Arrigo; John Dean; Corinne De Laet; Claudine De Praeter; Catherine Dery; Colin D Ferrie; Kim Flintoff; Suzanna G M Frints; Angels Garcia-Cazorla; Blanca Gener; Cyril Goizet; Francoise Goutieres; Andrew J Green; Agnes Guet; Ben C J Hamel; Bruce E Hayward; Arvid Heiberg; Raoul C Hennekam; Marie Husson; Andrew P Jackson; Rasieka Jayatunga; Yong-Hui Jiang; Sarina G Kant; Amy Kao; Mary D King; Helen M Kingston; Joerg Klepper; Marjo S van der Knaap; Andrew J Kornberg; Dieter Kotzot; Wilfried Kratzer; Didier Lacombe; Lieven Lagae; Pierre Georges Landrieu; Giovanni Lanzi; Andrea Leitch; Ming J Lim; John H Livingston; Charles M Lourenco; E G Hermione Lyall; Sally A Lynch; Michael J Lyons; Daphna Marom; John P McClure; Robert McWilliam; Serge B Melancon; Leena D Mewasingh; Marie-Laure Moutard; Ken K Nischal; John R Ostergaard; Julie Prendiville; Magnhild Rasmussen; R Curtis Rogers; Dominique Roland; Elisabeth M Rosser; Kevin Rostasy; Agathe Roubertie; Amparo Sanchis; Raphael Schiffmann; Sabine Scholl-Burgi; Sunita Seal; Stavit A Shalev; C Sierra Corcoles; Gyan P Sinha; Doriette Soler; Ronen Spiegel; John B P Stephenson; Uta Tacke; Tiong Yang Tan; Marianne Till; John L Tolmie; Pam Tomlin; Federica Vagnarelli; Enza Maria Valente; Rudy N A Van Coster; Nathalie Van der Aa; Adeline Vanderver; Johannes S H Vles; Thomas Voit; Evangeline Wassmer; Bernhard Weschke; Margo L Whiteford; Michel A A Willemsen; Andreas Zankl; Sameer M Zuberi; Simona Orcesi; Elisa Fazzi; Pierre Lebon; Yanick J Crow
Journal:  Am J Hum Genet       Date:  2007-09-04       Impact factor: 11.025

5.  JAK1/2 inhibition with baricitinib in the treatment of autoinflammatory interferonopathies.

Authors:  Gina A Montealegre Sanchez; Adam Reinhardt; Suzanne Ramsey; Helmut Wittkowski; Philip J Hashkes; Yackov Berkun; Susanne Schalm; Sara Murias; Jason A Dare; Diane Brown; Deborah L Stone; Ling Gao; Thomas Klausmeier; Dirk Foell; Adriana A de Jesus; Dawn C Chapelle; Hanna Kim; Samantha Dill; Robert A Colbert; Laura Failla; Bahar Kost; Michelle O'Brien; James C Reynolds; Les R Folio; Katherine R Calvo; Scott M Paul; Nargues Weir; Alessandra Brofferio; Ariane Soldatos; Angelique Biancotto; Edward W Cowen; John J Digiovanna; Massimo Gadina; Andrew J Lipton; Colleen Hadigan; Steven M Holland; Joseph Fontana; Ahmad S Alawad; Rebecca J Brown; Kristina I Rother; Theo Heller; Kristina M Brooks; Parag Kumar; Stephen R Brooks; Meryl Waldman; Harsharan K Singh; Volker Nickeleit; Maria Silk; Apurva Prakash; Jonathan M Janes; Seza Ozen; Paul G Wakim; Paul A Brogan; William L Macias; Raphaela Goldbach-Mansky
Journal:  J Clin Invest       Date:  2018-06-11       Impact factor: 14.808

  5 in total
  28 in total

1.  DNA damage contributes to neurotoxic inflammation in Aicardi-Goutières syndrome astrocytes.

Authors:  Marco Luciani; Francesca Gatto; Monah Abou Alezz; Anna Maria Sole Giordano; Chiara Beghè; Lucrezia Della Volpe; Alessandro Migliara; Sara Valsoni; Marco Genua; Monika Dzieciatkowska; Giacomo Frati; Julie Tahraoui-Bories; Silvia Clara Giliani; Simona Orcesi; Elisa Fazzi; Renato Ostuni; Angelo D'Alessandro; Raffaella Di Micco; Ivan Merelli; Angelo Lombardo; Martin A M Reijns; Natalia Gromak; Angela Gritti; Anna Kajaste-Rudnitski
Journal:  J Exp Med       Date:  2022-03-09       Impact factor: 14.307

Review 2.  Pathogenic insights from genetic causes of autoinflammatory inflammasomopathies and interferonopathies.

Authors:  Bin Lin; Raphaela Goldbach-Mansky
Journal:  J Allergy Clin Immunol       Date:  2021-12-08       Impact factor: 10.793

Review 3.  No Longer A One-Trick Pony: STING Signaling Activity Beyond Interferon.

Authors:  Jianjun Wu; Nan Yan
Journal:  J Mol Biol       Date:  2021-10-08       Impact factor: 5.469

4.  Hematologic abnormalities in Aicardi Goutières Syndrome.

Authors:  Laura A Adang; Francesco Gavazzi; Russell D'Aiello; David Isaacs; Nowa Bronner; Zehra Serap Arici; Zaida Flores; Amanda Jan; Carly Scher; Omar Sherbini; Edward M Behrens; Raphaela Goldbach-Mansky; Timothy S Olson; Michele P Lambert; Kathleen E Sullivan; David T Teachey; Char Witmer; Adeline Vanderver; Justine Shults
Journal:  Mol Genet Metab       Date:  2022-06-16       Impact factor: 4.204

Review 5.  Safety updates in novel therapeutics for pediatric rheumatic disease.

Authors:  Rachel L Randell; Mara L Becker
Journal:  Curr Opin Rheumatol       Date:  2021-09-01       Impact factor: 4.941

Review 6.  Emerging concepts of type I interferons in SLE pathogenesis and therapy.

Authors:  Antonios Psarras; Miriam Wittmann; Edward M Vital
Journal:  Nat Rev Rheumatol       Date:  2022-09-12       Impact factor: 32.286

7.  Effectiveness and Safety of JAK Inhibitors in Autoinflammatory Diseases: A Systematic Review.

Authors:  Zhivana Boyadzhieva; Nikolas Ruffer; Gerd Burmester; Anne Pankow; Martin Krusche
Journal:  Front Med (Lausanne)       Date:  2022-06-27

8.  Hepatic Involvement in Aicardi-Goutières Syndrome.

Authors:  Francesco Gavazzi; Zachary M Cross; Sarah Woidill; Joseph M McMann; Elizabeth B Rand; Asako Takanohashi; Nicole Ulrick; Justine Shults; Adeline L Vanderver; Laura Adang
Journal:  Neuropediatrics       Date:  2021-01-14       Impact factor: 1.947

9.  Ruxolitinib in Aicardi-Goutières syndrome.

Authors:  Eleonora Mura; Silvia Masnada; Clara Antonello; Cecilia Parazzini; Giana Izzo; Jessica Garau; Daisy Sproviero; Cristina Cereda; Simona Orcesi; Pierangelo Veggiotti; Gianvincenzo Zuccotti; Dario Dilillo; Francesca Penagini; Davide Tonduti
Journal:  Metab Brain Dis       Date:  2021-03-15       Impact factor: 3.584

Review 10.  Vasculitis, Autoimmunity, and Cytokines: How the Immune System Can Harm the Brain.

Authors:  Alessandra Tesser; Alessia Pin; Elisabetta Mencaroni; Virginia Gulino; Alberto Tommasini
Journal:  Int J Environ Res Public Health       Date:  2021-05-24       Impact factor: 3.390

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