Literature DB >> 32770851

Real-world long-term effectiveness of ustekinumab in Crohn's disease: results from the ENEIDA registry.

Marisa Iborra1, Belén Beltrán1, Agnes Fernández-Clotet2, Eva Iglesias-Flores3, Pablo Navarro1, Montserrat Rivero4, Ana Gutiérrez5, Mónica Sierra-Ausin6, Francisco Mesonero7, Rocío Ferreiro-Iglesias8, Joaquín Hinojosa1, Xavier Calvet2, Beatriz Sicilia9, Carlos González-Muñoza2, Beatriz Antolín10, María González-Vivo2, Ana Y Carbajo10, Santiago García-López11, Albert Martín-Cardona2, Gerard Surís2, María Dolores Martin-Arranz7, Ruth de Francisco12, Fiorella Cañete2, Eugeni Domènech2, Pilar Nos1.   

Abstract

BACKGROUND: Data on the long-term administration of ustekinumab in recommended doses are limited. AIM: To assess the real-world, long-term effectiveness of ustekinumab in refractory Crohn's disease (CD).
METHODS: Multi-centre study of CD patients starting ustekinumab at the recommended dose, followed for 1 year. Values for the Harvey-Bradshaw Index (HBI), endoscopic activity, C-reactive protein (CRP), and faecal calprotectin (FC) were recorded at baseline and at weeks 26 and 52. Demographic and clinical data, previous treatments, adverse events (AEs) and hospitalisations were documented. Potential predictors of remission were examined.
RESULTS: A total of 407 patients were analysed. The initial maintenance dose of 90 mg SC was administered every 12, 8 and 4 weeks in 56 (14%), 347 (85%) and 4 (1%) patients, respectively. After 52 weeks, treatment was discontinued in 112 patients (27.5%). At baseline, 295 (72%) had an HBI >4 points. Of these, 169 (57%) and 190 (64%) achieved clinical remission at weeks 26 and 52, respectively. FC levels returned to normal in 44% and 54% of patients at weeks 26 and 52, and CRP returned to normal in 36% and 37% of patients at weeks 26 and 52, respectively. AEs were recorded in 60 patients. The use of fewer previous anti-TNFα agents and ileal localisation were associated with clinical remission, and endoscopic severity was associated with poor response. No factors correlated with endoscopic remission.
CONCLUSION: After 52 weeks, ustekinumab demonstrated effectiveness in inducing clinical and endoscopic remission in patients with refractory CD.
© 2020 John Wiley & Sons Ltd.

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Year:  2020        PMID: 32770851     DOI: 10.1111/apt.15958

Source DB:  PubMed          Journal:  Aliment Pharmacol Ther        ISSN: 0269-2813            Impact factor:   8.171


  8 in total

1.  Ustekinumab Is Associated with Real-World Long-Term Effectiveness and Improved Health-Related Quality of Life in Crohn's Disease.

Authors:  Jonas Halfvarson; Jonas F Ludvigsson; Anders Forss; Mark Clements; Pär Myrelid; Hans Strid; Charlotte Söderman; Agnieszka Wagner; David Andersson; Fredrik Hjelm; Ola Olén
Journal:  Dig Dis Sci       Date:  2022-04-22       Impact factor: 3.199

Review 2.  How to Optimize Treatment With Ustekinumab in Inflammatory Bowel Disease: Lessons Learned From Clinical Trials and Real-World Data.

Authors:  Ana Gutiérrez; Iago Rodríguez-Lago
Journal:  Front Med (Lausanne)       Date:  2021-01-28

3.  Effectiveness of ustekinumab in patients with refractory Crohn's disease: a multicentre real-life study in Italy.

Authors:  Maria Lia Scribano; Annalisa Aratari; Benedetto Neri; Cristina Bezzio; Paola Balestrieri; Valentina Baccolini; Giuliano Falasco; Caterina Camastra; Paolo Pantanella; Rita Monterubbianesi; Alessandro Tullio; Simone Saibeni; Claudio Papi; Livia Biancone; Rocco Cosintino; Roberto Faggiani
Journal:  Therap Adv Gastroenterol       Date:  2022-02-14       Impact factor: 4.409

Review 4.  Ileal and colonic Crohn's disease: Does location makes a difference in therapy efficacy?

Authors:  Raja Atreya; Christian Bojarski; Anja A Kühl; Zlatko Trajanoski; Markus F Neurath; Britta Siegmund
Journal:  Curr Res Pharmacol Drug Discov       Date:  2022-03-19

Review 5.  Ustekinumab in Crohn's Disease: New Data for Positioning in Treatment Algorithm.

Authors:  Ferdinando D'Amico; Laurent Peyrin-Biroulet; Silvio Danese
Journal:  J Crohns Colitis       Date:  2022-05-11       Impact factor: 10.020

6.  Using Interpretable Machine Learning to Identify Baseline Predictive Factors of Remission and Drug Durability in Crohn's Disease Patients on Ustekinumab.

Authors:  María Chaparro; Iria Baston-Rey; Estela Fernández Salgado; Javier González García; Laura Ramos; María Teresa Diz-Lois Palomares; Federico Argüelles-Arias; Eva Iglesias Flores; Mercedes Cabello; Saioa Rubio Iturria; Andrea Núñez Ortiz; Mara Charro; Daniel Ginard; Carmen Dueñas Sadornil; Olga Merino Ochoa; David Busquets; Eduardo Iyo; Ana Gutiérrez Casbas; Patricia Ramírez de la Piscina; Marta Maia Boscá-Watts; Maite Arroyo; María José García; Esther Hinojosa; Jordi Gordillo; Pilar Martínez Montiel; Benito Velayos Jiménez; Cristina Quílez Ivorra; Juan María Vázquez Morón; José María Huguet; Yago González-Lama; Ana Isabel Muñagorri Santos; Víctor Manuel Amo; María Dolores Martín Arranz; Fernando Bermejo; Jesús Martínez Cadilla; Cristina Rubín de Célix; Paola Fradejas Salazar; Antonio López San Román; Nuria Jiménez; Santiago García-López; Anna Figuerola; Itxaso Jiménez; Francisco José Martínez Cerezo; Carlos Taxonera; Pilar Varela; Ruth de Francisco; David Monfort; Gema Molina Arriero; Alejandro Hernández-Camba; Francisco Javier García Alonso; Manuel Van Domselaar; Ramón Pajares-Villarroya; Alejandro Núñez; Francisco Rodríguez Moranta; Ignacio Marín-Jiménez; Virginia Robles Alonso; María Del Mar Martín Rodríguez; Patricia Camo-Monterde; Iván García Tercero; Mercedes Navarro-Llavat; Lara Arias García; Daniel Hervías Cruz; Sebastian Kloss; Alun Passey; Cynthia Novella; Eugenia Vispo; Manuel Barreiro-de Acosta; Javier P Gisbert
Journal:  J Clin Med       Date:  2022-08-03       Impact factor: 4.964

7.  A propensity score-matched, real-world comparison of ustekinumab vs vedolizumab as a second-line treatment for Crohn's disease. The Cross Pennine study II.

Authors:  Marco Vincenzo Lenti; Vivien Dolby; Tanya Clark; Veronica Hall; Suzanne Tattersall; Francesca Fairhurst; Catherine Kenneth; Rachael Walker; Karen Kemp; Simon Borg-Bartolo; Jimmy K Limdi; Jo Taylor; Tristan Townsend; Sree Subramanian; Daniel Storey; Arash Assadsangabi; Catherine Stansfield; Paul Smith; Debra Byrne; Annalisa De Silvestri; Christian P Selinger
Journal:  Aliment Pharmacol Ther       Date:  2021-12-22       Impact factor: 9.524

Review 8.  Real-World Evidence of the Effectiveness and Safety of Ustekinumab for the Treatment of Crohn's Disease: Systematic Review and Meta-Analysis of Observational Studies.

Authors:  Cristina Rubín de Célix; María Chaparro; Javier P Gisbert
Journal:  J Clin Med       Date:  2022-07-20       Impact factor: 4.964

  8 in total

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