Literature DB >> 32671401

Gene therapy for global brain diseases: one small step for mice, one giant leap for humans.

Ahad A Rahim1, Paul Gissen2,3.   

Abstract

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Year:  2020        PMID： 32671401      PMCID： PMC7364739          DOI： 10.1093/brain/awaa189

Source DB:  PubMed          Journal:  Brain        ISSN： 0006-8950            Impact factor:   13.501


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  8 in total

Review 1.  Size and shape of the cerebral cortex in mammals. II. The cortical volume.

Authors:  M A Hofman
Journal:  Brain Behav Evol       Date:  1988       Impact factor: 1.808

2.  A Golgi study of the sixth layer of the cerebral cortex. II. The gyrencephalic brain of Carnivora, Artiodactyla and Primates.

Authors:  I Ferrer; I Fabregues; E Condom
Journal:  J Anat       Date:  1986-06       Impact factor: 2.610

3.  Size and shape of the cerebral cortex in mammals. I. The cortical surface.

Authors:  M A Hofman
Journal:  Brain Behav Evol       Date:  1985       Impact factor: 1.808

4.  Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.

Authors:  Jerry R Mendell; Samiah Al-Zaidy; Richard Shell; W Dave Arnold; Louise R Rodino-Klapac; Thomas W Prior; Linda Lowes; Lindsay Alfano; Katherine Berry; Kathleen Church; John T Kissel; Sukumar Nagendran; James L'Italien; Douglas M Sproule; Courtney Wells; Jessica A Cardenas; Marjet D Heitzer; Allan Kaspar; Sarah Corcoran; Lyndsey Braun; Shibi Likhite; Carlos Miranda; Kathrin Meyer; K D Foust; Arthur H M Burghes; Brian K Kaspar
Journal:  N Engl J Med       Date:  2017-11-02       Impact factor: 91.245

5.  Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy.

Authors:  Sea Young Yoon; Jacqueline E Hunter; Sanjeev Chawla; Dana L Clarke; Caitlyn Molony; Patricia A O'Donnell; Jessica H Bagel; Manoj Kumar; Harish Poptani; Charles H Vite; John H Wolfe
Journal:  Brain       Date:  2020-07-01       Impact factor: 13.501

6.  A Golgi study of the sixth layer of the cerebral cortex. I. The lissencephalic brain of Rodentia, Lagomorpha, Insectivora and Chiroptera.

Authors:  I Ferrer; I Fabregues; E Condom
Journal:  J Anat       Date:  1986-04       Impact factor: 2.610

7.  Expanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain.

Authors:  Cassia N Cearley; Luk H Vandenberghe; Michael K Parente; Erin R Carnish; James M Wilson; John H Wolfe
Journal:  Mol Ther       Date:  2008-08-19       Impact factor: 11.454

8.  Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.

Authors:  Amit C Nathwani; Edward G D Tuddenham; Savita Rangarajan; Cecilia Rosales; Jenny McIntosh; David C Linch; Pratima Chowdary; Anne Riddell; Arnulfo Jaquilmac Pie; Chris Harrington; James O'Beirne; Keith Smith; John Pasi; Bertil Glader; Pradip Rustagi; Catherine Y C Ng; Mark A Kay; Junfang Zhou; Yunyu Spence; Christopher L Morton; James Allay; John Coleman; Susan Sleep; John M Cunningham; Deokumar Srivastava; Etiena Basner-Tschakarjan; Federico Mingozzi; Katherine A High; John T Gray; Ulrike M Reiss; Arthur W Nienhuis; Andrew M Davidoff
Journal:  N Engl J Med       Date:  2011-12-10       Impact factor: 176.079
  8 in total
  1 in total

1.  Transduction characteristics of alternative adeno-associated virus serotypes in the cat brain by intracisternal delivery.

Authors:  Jacqueline E Hunter; Caitlyn M Molony; Jessica H Bagel; Patricia A O'Donnell; Stephen G Kaler; John H Wolfe
Journal:  Mol Ther Methods Clin Dev       Date:  2022-07-16       Impact factor: 5.849
  1 in total

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