Literature DB >> 32654954

Fifteen-year follow-up of a patient with a DHDDS variant with non-progressive early onset myoclonic tremor and rare generalized epilepsy.

Noriko Togashi1, Atsushi Fujita2, Moriei Shibuya1, Saki Uneoka1, Takuya Miyabayashi1, Ryo Sato1, Yukimune Okubo1, Wakaba Endo1, Takehiko Inui1, Kazutaka Jin3, Naomichi Matsumoto2, Kazuhiro Haginoya4.   

Abstract

BACKGROUND: Generalized epilepsy and tremor phenotypes have been reported in some genetic disorders. Among them benign adult familial myoclonus epilepsy (BAFME) has been confirmed as a clearly defined clinical and genetic entity. On the other hand, non-progressive tremor and generalized epilepsy phenotypes have also been reported in patients with DHDDS variants. CASE
PRESENTATION: We report on a long term follow-up of patient with de novo missense variant of DHDDS, who revealed non progressive nature. This 18-year-old woman presented non-progressive tremor since her early infancy. She had rare seizures. Her tremor was considered as cortical myoclonic tremor with giant somatosensory evoked potentials.
CONCLUSION: In patients with early onset, non-progressive tremor and rare generalized epilepsy phenotypes, DHDDS variants may be considered in the genetic differential diagnosis.
Copyright © 2020 The Japanese Society of Child Neurology. Published by Elsevier B.V. All rights reserved.

Entities:  

Keywords:  BAFME; Benign adult familial myoclonus epilepsy; DHDDS; Dystonia; Generalized epilepsy; Myoclonic tremor

Mesh:

Substances:

Year:  2020        PMID: 32654954     DOI: 10.1016/j.braindev.2020.06.011

Source DB:  PubMed          Journal:  Brain Dev        ISSN: 0387-7604            Impact factor:   1.961


  3 in total

1.  Progressive myoclonus epilepsies-Residual unsolved cases have marked genetic heterogeneity including dolichol-dependent protein glycosylation pathway genes.

Authors:  Carolina Courage; Karen L Oliver; Eon Joo Park; Jillian M Cameron; Kariona A Grabińska; Mikko Muona; Laura Canafoglia; Antonio Gambardella; Edith Said; Zaid Afawi; Betul Baykan; Christian Brandt; Carlo di Bonaventura; Hui Bein Chew; Chiara Criscuolo; Leanne M Dibbens; Barbara Castellotti; Patrizia Riguzzi; Angelo Labate; Alessandro Filla; Anna T Giallonardo; Geza Berecki; Christopher B Jackson; Tarja Joensuu; John A Damiano; Sara Kivity; Amos Korczyn; Aarno Palotie; Pasquale Striano; Davide Uccellini; Loretta Giuliano; Eva Andermann; Ingrid E Scheffer; Roberto Michelucci; Melanie Bahlo; Silvana Franceschetti; William C Sessa; Samuel F Berkovic; Anna-Elina Lehesjoki
Journal:  Am J Hum Genet       Date:  2021-04-01       Impact factor: 11.025

2.  De novo DHDDS variants cause a neurodevelopmental and neurodegenerative disorder with myoclonus.

Authors:  Serena Galosi; Ban H Edani; Simone Martinelli; Hana Hansikova; Erik A Eklund; Caterina Caputi; Laura Masuelli; Nicole Corsten-Janssen; Myriam Srour; Renske Oegema; Daniëlle G M Bosch; Colin A Ellis; Louise Amlie-Wolf; Andrea Accogli; Isis Atallah; Luisa Averdunk; Kristin W Barañano; Roberto Bei; Irene Bagnasco; Alfredo Brusco; Scott Demarest; Anne-Sophie Alaix; Carlo Di Bonaventura; Felix Distelmaier; Frances Elmslie; Ziv Gan-Or; Jean-Marc Good; Karen Gripp; Erik-Jan Kamsteeg; Ellen Macnamara; Carlo Marcelis; Noëlle Mercier; Joseph Peeden; Simone Pizzi; Luca Pannone; Marwan Shinawi; Camilo Toro; Nienke E Verbeek; Sunita Venkateswaran; Patricia G Wheeler; Lucie Zdrazilova; Rong Zhang; Giovanna Zorzi; Renzo Guerrini; William C Sessa; Dirk J Lefeber; Marco Tartaglia; Fadi F Hamdan; Kariona A Grabińska; Vincenzo Leuzzi
Journal:  Brain       Date:  2022-03-29       Impact factor: 15.255

3.  Adult-onset rapidly worsening progressive myoclonic epilepsy caused by a novel variant in DHDDS.

Authors:  Seondeuk Kim; Man Jin Kim; Hyoshin Son; Sungeun Hwang; Mi-Kyoung Kang; Kon Chu; Sang Kun Lee; Jangsup Moon
Journal:  Ann Clin Transl Neurol       Date:  2021-11-27       Impact factor: 4.511

  3 in total

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