Literature DB >> 32562673

Natural history data in adults with SMA.

Juan F Vázquez-Costa1.   

Abstract

Entities:  

Year:  2020        PMID: 32562673     DOI: 10.1016/S1474-4422(20)30183-6

Source DB:  PubMed          Journal:  Lancet Neurol        ISSN: 1474-4422            Impact factor:   44.182


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  2 in total

1.  Nusinersen in Adults with 5q Spinal Muscular Atrophy: a Systematic Review and Meta-analysis.

Authors:  Maria Gavriilaki; Maria Moschou; Vasileios Papaliagkas; Konstantinos Notas; Evangelia Chatzikyriakou; Sotirios Papagiannopoulos; Marianthi Arnaoutoglou; Vasilios K Kimiskidis
Journal:  Neurotherapeutics       Date:  2022-02-17       Impact factor: 6.088

2.  Improving Care and Empowering Adults Living with SMA: A Call to Action in the New Treatment Era.

Authors:  Maggie C Walter; Claudia Chiriboga; Tina Duong; Nathalie Goemans; Anna Mayhew; Laëtitia Ouillade; Maryam Oskoui; Ros Quinlivan; Juan F Vázquez-Costa; John Vissing; Laurent Servais
Journal:  J Neuromuscul Dis       Date:  2021
  2 in total

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