Literature DB >> 32248695

Representativeness of the PIONEER-HF Clinical Trial Population in Patients Hospitalized With Heart Failure and Reduced Ejection Fraction.

Marat Fudim1,2, Sabina Sayeed1, Haolin Xu3, Roland A Matsouaka3, Paul A Heidenreich4, Eric J Velazquez5, Clyde W Yancy6, Gregg C Fonarow7, Adrian F Hernandez1,2, Adam D DeVore1,2.   

Abstract

BACKGROUND: In PIONEER-HF (Comparison of Sacubitril/Valsartan Versus Enalapril on Effect on NT-pro BNP in Patients Stabilized From an Acute Heart Failure Episode), the in-hospital initiation of sacubitril/valsartan in patients hospitalized for acute decompensated heart failure (ADHF) was well-tolerated and led to improved outcomes. We aim to determine the representativeness of the PIONEER-HF trial among patients hospitalized for ADHF using real-world data.
METHODS: The study population was derived from all patients discharged alive for ADHF in the Get With The Guidelines-HF registry from 2006 to 2018 with HF with reduced ejection fraction (HFrEF; all HFrEF with ADHF). We then determined the proportion of patients meeting PIONEER-HF eligibility criteria (PIONEER-HF eligible) and those meeting a set of limited eligibility criteria (actionable cohort). Rates of HF readmissions and all-cause mortality were then compared between the all HFrEF with ADHF, PIONEER-HF eligible, and actionable cohorts using linked Medicare claims data.
RESULTS: A total of 99 767 patients with HFrEF in Get With The Guidelines-HF were hospitalized for ADHF. PIONEER-HF inclusion criteria were met by 71 633 (71.8%) patients, and both inclusion and exclusion criteria were met by 20 704 (20.8%) patients. Further, 68 739 (68.9%) patients met the criteria for the actionable cohort. Among the Centers for Medicare and Medicaid-linked patients, the HF rehospitalization rate at 1 year was 35.1% (95% CI, 34.5-35.8) for all HFrEF with ADHF patients, 32.6% (95% CI, 31.3-33.9) for the PIONEER-HF eligible cohort, and 33.1% (95% CI, 32.3-33.9) for the actionable cohort. The 1-year all-cause mortality was 36.7% (95% CI, 36.1-7.4) for all HFrEF with ADHF patients, 31.6% (95% CI, 30.3-32.9) for the PIONEER-HF eligible cohort, and 32.2% (95% CI, 31.4-33.0) for the actionable cohort.
CONCLUSIONS: Patient characteristics and clinical outcomes for patients eligible for PIONEER-HF only modestly differ when compared with those encountered in routine practice, suggesting that the in-hospital initiation of sacubitril/valsartan should be routinely considered for patients with HFrEF hospitalized for ADHF.

Entities:  

Keywords:  brain natriuretic peptide; enalapril; heart failure; hospitalization; sacubitril valsartan

Mesh:

Substances:

Year:  2020        PMID: 32248695      PMCID: PMC8819257          DOI: 10.1161/CIRCHEARTFAILURE.119.006645

Source DB:  PubMed          Journal:  Circ Heart Fail        ISSN: 1941-3289            Impact factor:   8.790


  24 in total

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Authors:  Emelia J Benjamin; Paul Muntner; Alvaro Alonso; Marcio S Bittencourt; Clifton W Callaway; April P Carson; Alanna M Chamberlain; Alexander R Chang; Susan Cheng; Sandeep R Das; Francesca N Delling; Luc Djousse; Mitchell S V Elkind; Jane F Ferguson; Myriam Fornage; Lori Chaffin Jordan; Sadiya S Khan; Brett M Kissela; Kristen L Knutson; Tak W Kwan; Daniel T Lackland; Tené T Lewis; Judith H Lichtman; Chris T Longenecker; Matthew Shane Loop; Pamela L Lutsey; Seth S Martin; Kunihiro Matsushita; Andrew E Moran; Michael E Mussolino; Martin O'Flaherty; Ambarish Pandey; Amanda M Perak; Wayne D Rosamond; Gregory A Roth; Uchechukwu K A Sampson; Gary M Satou; Emily B Schroeder; Svati H Shah; Nicole L Spartano; Andrew Stokes; David L Tirschwell; Connie W Tsao; Mintu P Turakhia; Lisa B VanWagner; John T Wilkins; Sally S Wong; Salim S Virani
Journal:  Circulation       Date:  2019-03-05       Impact factor: 29.690

2.  Clinical practice update on heart failure 2019: pharmacotherapy, procedures, devices and patient management. An expert consensus meeting report of the Heart Failure Association of the European Society of Cardiology.

Authors:  Petar M Seferovic; Piotr Ponikowski; Stefan D Anker; Johann Bauersachs; Ovidiu Chioncel; John G F Cleland; Rudolf A de Boer; Heinz Drexel; Tuvia Ben Gal; Loreena Hill; Tiny Jaarsma; Ewa A Jankowska; Markus S Anker; Mitja Lainscak; Basil S Lewis; Theresa McDonagh; Marco Metra; Davor Milicic; Wilfried Mullens; Massimo F Piepoli; Giuseppe Rosano; Frank Ruschitzka; Maurizio Volterrani; Adriaan A Voors; Gerasimos Filippatos; Andrew J S Coats
Journal:  Eur J Heart Fail       Date:  2019-08-30       Impact factor: 15.534

3.  Hospitalist and primary care physician perspectives on medication management of chronic conditions for hospitalized patients.

Authors:  Anthony C Breu; Joshua Allen-Dicker; Stephanie Mueller; Kerri Palamara; Keiki Hinami; Shoshana J Herzig
Journal:  J Hosp Med       Date:  2014-02-24       Impact factor: 2.960

4.  Scope of Sacubitril/Valsartan Eligibility After Heart Failure Hospitalization: Findings From the GWTG-HF Registry (Get With The Guidelines-Heart Failure).

Authors:  Kishan S Parikh; Steven J Lippmann; Melissa Greiner; Paul A Heidenreich; Clyde W Yancy; Gregg C Fonarow; Adrian F Hernandez
Journal:  Circulation       Date:  2017-05-23       Impact factor: 29.690

Review 5.  Initiation, Continuation, Switching, and Withdrawal of Heart Failure Medical Therapies During Hospitalization.

Authors:  Aditi A Bhagat; Stephen J Greene; Muthiah Vaduganathan; Gregg C Fonarow; Javed Butler
Journal:  JACC Heart Fail       Date:  2018-11-07       Impact factor: 12.035

6.  Angiotensin-Neprilysin Inhibition in Acute Decompensated Heart Failure.

Authors:  Eric J Velazquez; David A Morrow; Adam D DeVore; Carol I Duffy; Andrew P Ambrosy; Kevin McCague; Ricardo Rocha; Eugene Braunwald
Journal:  N Engl J Med       Date:  2018-11-11       Impact factor: 91.245

7.  2019 ACC Expert Consensus Decision Pathway on Risk Assessment, Management, and Clinical Trajectory of Patients Hospitalized With Heart Failure: A Report of the American College of Cardiology Solution Set Oversight Committee.

Authors:  Steven M Hollenberg; Lynne Warner Stevenson; Tariq Ahmad; Vaibhav J Amin; Biykem Bozkurt; Javed Butler; Leslie L Davis; Mark H Drazner; James N Kirkpatrick; Pamela N Peterson; Brent N Reed; Christopher L Roy; Alan B Storrow
Journal:  J Am Coll Cardiol       Date:  2019-09-13       Impact factor: 24.094

8.  Effect of Optimizing Guideline-Directed Medical Therapy Before Discharge on Mortality and Heart Failure Readmission in Patients Hospitalized With Heart Failure With Reduced Ejection Fraction.

Authors:  Tetsuo Yamaguchi; Takeshi Kitai; Takamichi Miyamoto; Nobuyuki Kagiyama; Takahiro Okumura; Keisuke Kida; Shogo Oishi; Eiichi Akiyama; Satoshi Suzuki; Masayoshi Yamamoto; Junji Yamaguchi; Takamasa Iwai; Sadahiro Hijikata; Ryo Masuda; Ryoichi Miyazaki; Nobuhiro Hara; Yasutoshi Nagata; Toshihiro Nozato; Yuya Matsue
Journal:  Am J Cardiol       Date:  2018-02-21       Impact factor: 2.778

9.  Titration of Medical Therapy for Heart Failure With Reduced Ejection Fraction.

Authors:  Stephen J Greene; Gregg C Fonarow; Adam D DeVore; Puza P Sharma; Muthiah Vaduganathan; Nancy M Albert; Carol I Duffy; C Larry Hill; Kevin McCague; J Herbert Patterson; John A Spertus; Laine Thomas; Fredonia B Williams; Adrian F Hernandez; Javed Butler
Journal:  J Am Coll Cardiol       Date:  2019-03-04       Impact factor: 24.094

10.  Cardiovascular biomarkers in patients with acute decompensated heart failure randomized to sacubitril-valsartan or enalapril in the PIONEER-HF trial.

Authors:  David A Morrow; Eric J Velazquez; Adam D DeVore; Margaret F Prescott; Carol I Duffy; Yared Gurmu; Kevin McCague; Ricardo Rocha; Eugene Braunwald
Journal:  Eur Heart J       Date:  2019-10-21       Impact factor: 29.983

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3.  Applicability of US Food and Drug Administration Labeling for Dapagliflozin to Patients With Heart Failure With Reduced Ejection Fraction in US Clinical Practice: The Get With the Guidelines-Heart Failure (GWTG-HF) Registry.

Authors:  Muthiah Vaduganathan; Stephen J Greene; Shuaiqi Zhang; Maria Grau-Sepulveda; Adam D DeVore; Javed Butler; Paul A Heidenreich; Joanna C Huang; Michelle M Kittleson; Karen E Joynt Maddox; James J McDermott; Anjali Tiku Owens; Pamela N Peterson; Scott D Solomon; Orly Vardeny; Clyde W Yancy; Gregg C Fonarow
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Review 4.  Factors associated with non-use and sub-target dosing of medical therapy for heart failure with reduced ejection fraction.

Authors:  Stephen J Greene; Xi Tan; Yu-Chen Yeh; Mark Bernauer; Omer Zaidi; Mei Yang; Javed Butler
Journal:  Heart Fail Rev       Date:  2021-01-20       Impact factor: 4.214

Review 5.  Angiotensin receptor-neprilysin inhibition in patients with acute decompensated heart failure: an expert consensus position paper.

Authors:  Argyrios Ntalianis; Christina Chrysohoou; George Giannakoulas; Grigorios Giamouzis; Apostolos Karavidas; Aikaterini Naka; Constantinos H Papadopoulos; Sotirios Patsilinakos; John Parissis; Dimitrios Tziakas; John Kanakakis
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Review 6.  New Strategies to Prevent Rehospitalizations for Heart Failure.

Authors:  Jamie Diamond; Adam D DeVore
Journal:  Curr Treat Options Cardiovasc Med       Date:  2022-09-22

7.  Representativeness of the GALACTIC-HF Clinical Trial in Patients Having Heart Failure With Reduced Ejection Fraction.

Authors:  Matthew T Mefford; Sandra Y Koyama; Justine De Jesus; Rong Wei; Heidi Fischer; Teresa N Harrison; Pauline Woo; Kristi Reynolds
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Review 8.  Sex-Related Differences in Dilated Cardiomyopathy with a Focus on Cardiac Dysfunction in Oncology.

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