Literature DB >> 32199087

Nusinersen in adults with spinal muscular atrophy: new challenges.

Eugenio Mercuri1, Valeria Sansone2.   

Abstract

Entities:  

Year:  2020        PMID： 32199087     DOI： 10.1016/S1474-4422(20)30068-5

Source DB:  PubMed          Journal:  Lancet Neurol        ISSN： 1474-4422            Impact factor:   44.182


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  6 in total

Review 1.  Spinal muscular atrophy - insights and challenges in the treatment era.

Authors:  Eugenio Mercuri; Maria Carmela Pera; Mariacristina Scoto; Richard Finkel; Francesco Muntoni
Journal:  Nat Rev Neurol       Date:  2020-10-14       Impact factor: 42.937

2.  Quality of life assessment in adult spinal muscular atrophy patients treated with nusinersen.

Authors:  Silvia Bonanno; Riccardo Zanin; Luca Bello; Irene Tramacere; Virginia Bozzoni; Luca Caumo; Manfredi Ferraro; Sara Bortolani; Gianni Sorarù; Mauro Silvestrini; Veria Vacchiano; Mara Turri; Raffaella Tanel; Rocco Liguori; Michela Coccia; Renato Emilio Mantegazza; Tiziana Mongini; Elena Pegoraro; Lorenzo Maggi
Journal:  J Neurol       Date:  2022-01-03       Impact factor: 4.849

Review 3.  Drug Screening and Drug Repositioning as Promising Therapeutic Approaches for Spinal Muscular Atrophy Treatment.

Authors:  Giovanna Menduti; Daniela Maria Rasà; Serena Stanga; Marina Boido
Journal:  Front Pharmacol       Date:  2020-11-12       Impact factor: 5.810

4.  Nusinersen: A Review in 5q Spinal Muscular Atrophy.

Authors:  Sheridan M Hoy
Journal:  CNS Drugs       Date:  2021-11-30       Impact factor: 5.749

5.  Improving Care and Empowering Adults Living with SMA: A Call to Action in the New Treatment Era.

Authors:  Maggie C Walter; Claudia Chiriboga; Tina Duong; Nathalie Goemans; Anna Mayhew; Laëtitia Ouillade; Maryam Oskoui; Ros Quinlivan; Juan F Vázquez-Costa; John Vissing; Laurent Servais
Journal:  J Neuromuscul Dis       Date:  2021

6.  A Canadian Adult Spinal Muscular Atrophy Outcome Measures Toolkit: Results of a National Consensus using a Modified Delphi Method.

Authors:  Jeremy Slayter; Victoria Hodgkinson; Josh Lounsberry; Bernard Brais; Kristine Chapman; Angela Genge; Aaron Izenberg; Wendy Johnston; Hanns Lochmüller; Erin O'Ferrall; Gerald Pfeffer; Stephanie Plamondon; Xavier Rodrigue; Kerri Schellenberg; Christen Shoesmith; Christine Stables; Monique Taillon; Jodi Warman-Chardon; Lawrence Korngut; Colleen O'Connell
Journal:  J Neuromuscul Dis       Date:  2021
  6 in total

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