| Literature DB >> 32052936 |
Pauline Le Van Quyen1, Nadège Calmels2,3, Maryse Bonnière4, Suzanne Chartier4, Féréchté Razavi4, Jamel Chelly2, Salima El Chehadeh5, Sarah Baer5, Lucile Boutaud4,6, Séverine Bacrot4, Cathy Obringer3, Romain Favre7, Tania Attié-Bitach4,6, Vincent Laugel3,8, Maria C Antal1,9.
Abstract
Cerebro-oculo-facio-skeletal syndrome (COFS) is a rare autosomal recessive neurodegenerative disease belonging to the family of DNA repair disorders, characterized by microcephaly, congenital cataracts, facial dysmorphism and arthrogryposis. Here, we describe the detailed morphological and microscopic phenotype of three fetuses from two families harboring ERCC5/XPG likely pathogenic variants, and review the five previously reported fetal cases. In addition to the classical features of COFS, the fetuses display thymus hyperplasia, splenomegaly and increased hematopoiesis. Microencephaly is present in the three fetuses with delayed development of the gyri, but normal microscopic anatomy at the supratentorial level. Microscopic anomalies reminiscent of pontocerebellar hypoplasia are present at the infratentorial level. In conclusion, COFS syndrome should be considered in fetuses when intrauterine growth retardation is associated with microcephaly, arthrogryposis and ocular anomalies. Further studies are needed to better understand XPG functions during human development.Entities:
Keywords: COFS; ERCC5; XPG; fetal pathology; neuropathology
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Year: 2020 PMID: 32052936 DOI: 10.1002/ajmg.a.61520
Source DB: PubMed Journal: Am J Med Genet A ISSN: 1552-4825 Impact factor: 2.802