Literature DB >> 31986515

A phase II trial of everolimus in patients with advanced pancreatic neuroendocrine carcinoma refractory or intolerant to platinum-containing chemotherapy (NECTOR trial).

Hiroyuki Okuyama, Masafumi Ikeda, Takuji Okusaka, Masayuki Furukawa, Shinichi Ohkawa, Ayumu Hosokawa, Yasushi Kojima, Hiroki Hara, Gou Murohisa, Kazuhiko Shioji, Akinori Asagi, Nobumasa Mizuno, Motohiro Kojima, Takeharu Yamanaka, Junji Furuse.   

Abstract

BACKGROUND: Platinum-containing regimens are widely used as first-line chemotherapy for unresectable pancreatic neuroendocrine carcinoma (NEC), but second-line chemotherapies have yet to be established.
OBJECTIVES: We evaluated the safety and efficacy of everolimus in patients with pancreatic NEC refractory or intolerant to platinum-containing chemotherapy.
METHODS: This study was a prospective, multicenter, phase II trial in patients with pancreatic NEC after platinum-containing chemotherapy. Everolimus treatment was continued until disease progression or intolerable toxicity was observed. The primary endpoint was progression-free survival (PFS).
RESULTS: Participants comprised 25 patients. Median age was 63 years, median PFS was 1.2 months [95% confidence interval (CI) 0.9-3.1 months], median overall survival was 7.5 months (95%CI 3.1- 13.5 months), overall response rate was 0%, and disease control rate was 39.1%. Common grade 3/4 adverse events were hyperglycemia (20%), thrombocytopenia (16%), and anemia (16%).
CONCLUSION: Efficacy of everolimus was limited in patients with unresectable pancreatic NEC. The Author(s). Published by S. Karger AG, Basel.

Entities:  

Year:  2020        PMID: 31986515     DOI: 10.1159/000505550

Source DB:  PubMed          Journal:  Neuroendocrinology        ISSN: 0028-3835            Impact factor:   4.914


  5 in total

1.  Identification of functional pathways and molecular signatures in neuroendocrine neoplasms by multi-omics analysis.

Authors:  Viola Melone; Annamaria Salvati; Domenico Palumbo; Giorgio Giurato; Giovanni Nassa; Francesca Rizzo; Luigi Palo; Alessandro Giordano; Mariarosaria Incoronato; Mario Vitale; Caterina Mian; Immacolata Di Biase; Stefano Cristiano; Viviana Narciso; Monica Cantile; Annabella Di Mauro; Fabiana Tatangelo; Salvatore Tafuto; Roberta Modica; Claudia Pivonello; Marco Salvatore; Annamaria Colao; Alessandro Weisz; Roberta Tarallo
Journal:  J Transl Med       Date:  2022-07-06       Impact factor: 8.440

2.  Emodin Reverses Gemcitabine Resistance of Pancreatic Cancer Cell Lines Through Inhibition of IKKβ/NF-κB Signaling Pathway.

Authors:  Hongfei Tong; Zhen Huang; Hui Chen; Bin Zhou; Yi Liao; Zhaohong Wang
Journal:  Onco Targets Ther       Date:  2020-10-02       Impact factor: 4.147

3.  First-line everolimus and cisplatin in patients with advanced extrapulmonary neuroendocrine carcinoma: a nationwide phase 2 single-arm clinical trial.

Authors:  Sonja Levy; Wieke H M Verbeek; Ferry A L M Eskens; José G van den Berg; Derk Jan A de Groot; Monique E van Leerdam; Margot E T Tesselaar
Journal:  Ther Adv Med Oncol       Date:  2022-02-27       Impact factor: 8.168

4.  Poor outcome after systemic therapy in secondary high-grade pancreatic neuroendocrine tumors.

Authors:  Kazhan Mollazadegan; Britt Skogseid; Johan Botling; Tobias Åkerström; Barbro Eriksson; Staffan Welin; Anders Sundin; Joakim Crona
Journal:  Endocr Connect       Date:  2022-03-14       Impact factor: 3.335

5.  Therapeutic strategies for gastroenteropancreatic neuroendocrine neoplasms: State-of-the-art and future perspectives.

Authors:  Elettra Merola; Andrea Michielan; Umberto Rozzanigo; Marco Erini; Sandro Sferrazza; Stefano Marcucci; Chiara Sartori; Chiara Trentin; Giovanni de Pretis; Franca Chierichetti
Journal:  World J Gastrointest Surg       Date:  2022-02-27
  5 in total

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