Literature DB >> 31964688

Preserved single muscle fiber specific force in facioscapulohumeral muscular dystrophy.

Saskia Lassche1, Nicol C Voermans2, Robbert van der Pijl2, Marloes van den Berg2, Arend Heerschap2, Hieronymus van Hees2, Benno Kusters2, Silvère M van der Maarel2, Coen A C Ottenheijm2, Baziel G M van Engelen2.   

Abstract

OBJECTIVE: To investigate single muscle fiber contractile performance in muscle biopsies from patients with facioscapulohumeral muscular dystrophy (FSHD), one of the most common hereditary muscle disorders.
METHODS: We collected 50 muscle biopsies (26 vastus lateralis, 24 tibialis anterior) from 14 patients with genetically confirmed FSHD and 12 healthy controls. Single muscle fibers (n = 547) were isolated for contractile measurements. Titin content and titin phosphorylation were examined in vastus lateralis muscle biopsies.
RESULTS: Single muscle fiber specific force was intact at saturating and physiologic calcium concentrations in all FSHD biopsies, with (FSHDFAT) and without (FSHDNORMAL) fatty infiltration, compared to healthy controls. Myofilament calcium sensitivity of force is increased in single muscle fibers obtained from FSHD muscle biopsies with increased fatty infiltration, but not in FSHD muscle biopsies without fatty infiltration (pCa50: 5.77-5.80 in healthy controls, 5.74-5.83 in FSHDNORMAL, and 5.86-5.90 in FSHDFAT single muscle fibers). Cross-bridge cycling kinetics at saturating calcium concentrations and myofilament cooperativity did not differ from healthy controls. Development of single muscle fiber passive tension was changed in all FSHD vastus lateralis and in FSHDFAT tibialis anterior, resulting in increased fiber stiffness. Titin content was increased in FSHD vastus lateralis biopsies; however, titin phosphorylation did not differ from healthy controls.
CONCLUSION: Muscle weakness in patients with FSHD is not caused by reduced specific force of individual muscle fibers, even in severely affected tissue with marked fatty infiltration of muscle tissue.
© 2020 American Academy of Neurology.

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Year:  2020        PMID: 31964688      PMCID: PMC7220237          DOI: 10.1212/WNL.0000000000008977

Source DB:  PubMed          Journal:  Neurology        ISSN: 0028-3878            Impact factor:   9.910


  35 in total

1.  Quantitative MR imaging of individual muscle involvement in facioscapulohumeral muscular dystrophy.

Authors:  Hermien E Kan; Tom W J Scheenen; Marielle Wohlgemuth; Dennis W J Klomp; Ivonne van Loosbroek-Wagenmans; George W Padberg; Arend Heerschap
Journal:  Neuromuscul Disord       Date:  2009-03-28       Impact factor: 4.296

2.  Population-based incidence and prevalence of facioscapulohumeral dystrophy.

Authors:  Johanna C W Deenen; Hisse Arnts; Silvère M van der Maarel; George W Padberg; Jan J G M Verschuuren; Egbert Bakker; Stephanie S Weinreich; André L M Verbeek; Baziel G M van Engelen
Journal:  Neurology       Date:  2014-08-13       Impact factor: 9.910

3.  DUX4 activates germline genes, retroelements, and immune mediators: implications for facioscapulohumeral dystrophy.

Authors:  Linda N Geng; Zizhen Yao; Lauren Snider; Abraham P Fong; Jennifer N Cech; Janet M Young; Silvere M van der Maarel; Walter L Ruzzo; Robert C Gentleman; Rabi Tawil; Stephen J Tapscott
Journal:  Dev Cell       Date:  2011-12-29       Impact factor: 12.270

4.  Mutations in DNMT3B Modify Epigenetic Repression of the D4Z4 Repeat and the Penetrance of Facioscapulohumeral Dystrophy.

Authors:  Marlinde L van den Boogaard; Richard J L F Lemmers; Judit Balog; Mariëlle Wohlgemuth; Mari Auranen; Satomi Mitsuhashi; Patrick J van der Vliet; Kirsten R Straasheijm; Rob F P van den Akker; Marjolein Kriek; Marlies E Y Laurense-Bik; Vered Raz; Monique M van Ostaijen-Ten Dam; Kerstin B M Hansson; Elly L van der Kooi; Sari Kiuru-Enari; Bjarne Udd; Maarten J D van Tol; Ichizo Nishino; Rabi Tawil; Stephen J Tapscott; Baziel G M van Engelen; Silvère M van der Maarel
Journal:  Am J Hum Genet       Date:  2016-05-05       Impact factor: 11.025

5.  Muscle pathology grade for facioscapulohumeral muscular dystrophy biopsies.

Authors:  Jeffrey M Statland; Bharati Shah; Don Henderson; Silvere Van Der Maarel; Stephen J Tapscott; Rabi Tawil
Journal:  Muscle Nerve       Date:  2015-06-18       Impact factor: 3.217

6.  PKC phosphorylation of titin's PEVK element: a novel and conserved pathway for modulating myocardial stiffness.

Authors:  Carlos Hidalgo; Bryan Hudson; Julius Bogomolovas; Yi Zhu; Brian Anderson; Marion Greaser; Siegfried Labeit; Henk Granzier
Journal:  Circ Res       Date:  2009-08-13       Impact factor: 17.367

7.  The DUX4 gene at the FSHD1A locus encodes a pro-apoptotic protein.

Authors:  Valeria Kowaljow; Aline Marcowycz; Eugénie Ansseau; Cecilia B Conde; Sébastien Sauvage; Christel Mattéotti; Cristina Arias; E Daniel Corona; Nicolás G Nuñez; Oberdan Leo; Ruddy Wattiez; Denise Figlewicz; Dalila Laoudj-Chenivesse; Alexandra Belayew; Frédérique Coppée; Alberto L Rosa
Journal:  Neuromuscul Disord       Date:  2007-06-27       Impact factor: 4.296

8.  Troponin activator augments muscle force in nemaline myopathy patients with nebulin mutations.

Authors:  Josine Marieke de Winter; Danielle Buck; Carlos Hidalgo; Jeffrey R Jasper; Fady I Malik; Nigel F Clarke; Ger J M Stienen; Michael W Lawlor; Alan H Beggs; Coen A C Ottenheijm; Henk Granzier
Journal:  J Med Genet       Date:  2013-04-09       Impact factor: 6.318

Review 9.  Sarcomere Dysfunction in Nemaline Myopathy.

Authors:  Josine M de Winter; Coen A C Ottenheijm
Journal:  J Neuromuscul Dis       Date:  2017

10.  MRI-Guided Biopsy as a Tool for Diagnosis and Research of Muscle Disorders.

Authors:  Saskia Lassche; Barbara H Janssen; Ties IJzermans; Jurgen J Fütterer; Nicol C Voermans; Arend Heerschap; Benno Küsters; Ritse M Mann; Baziel Gm van Engelen
Journal:  J Neuromuscul Dis       Date:  2018
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  3 in total

Review 1.  Systematic review of skeletal muscle passive mechanics experimental methodology.

Authors:  Benjamin I Binder-Markey; Danielle Sychowski; Richard L Lieber
Journal:  J Biomech       Date:  2021-10-26       Impact factor: 2.712

2.  Increased resistance towards fatigability in patients with facioscapulohumeral muscular dystrophy.

Authors:  Matteo Beretta-Piccoli; Luca Calanni; Massimo Negro; Giulia Ricci; Cinzia Bettio; Marco Barbero; Angela Berardinelli; Gabriele Siciliano; Rossella Tupler; Emiliano Soldini; Corrado Cescon; Giuseppe D'Antona
Journal:  Eur J Appl Physiol       Date:  2021-03-01       Impact factor: 3.078

3.  Reduced specific force in patients with mild and severe facioscapulohumeral muscular dystrophy.

Authors:  Saskia Lassche; Nicol C Voermans; Tim Schreuder; Arend Heerschap; Benno Küsters; Coen Ac Ottenheijm; Maria Te Hopman; Baziel Gm van Engelen
Journal:  Muscle Nerve       Date:  2020-10-15       Impact factor: 3.217

  3 in total

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