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Abstract
Entities: Disease
Mesh: See more » Aminophenols/therapeutic useBenzodioxoles/therapeutic useCystic Fibrosis/drug therapyCystic Fibrosis/geneticsCystic Fibrosis/pathologyCystic Fibrosis Transmembrane Conductance Regulator/geneticsDrug ApprovalDrug CombinationsHumansIndoles/therapeutic usePyrazoles/therapeutic usePyridines/therapeutic usePyrrolidines/therapeutic useQuinolines/therapeutic useQuinolones/therapeutic useUnited States/epidemiologyUnited States Food and Drug Administration
Substances: See more » AminophenolsBenzodioxolesCFTR protein, humanDrug CombinationsIndolesPyrazolesPyridinesPyrrolidinesQuinolinesQuinoloneselexcaftor, ivacaftor, tezacaftor drug combinationtezacaftorCystic Fibrosis Transmembrane Conductance Regulatorivacaftorelexacaftor
Year: 2020 PMID: 31825178 DOI: 10.1002/ajmg.a.61420
Source DB: PubMed Journal: Am J Med Genet A ISSN: 1552-4825 Impact factor: 2.802