Literature DB >> 31813083

Advances Toward Precision Medicine in Juvenile Dermatomyositis.

Jessica Neely1, Susan Kim2.   

Abstract

PURPOSE OF REVIEW: We seek to provide a summary of the recent advances in juvenile dermatomyositis (JDM) that are moving the field toward precision care and personalized medicine for this uncommon condition. RECENT
FINDINGS: There has been a recent international focus on developing uniform classification, disease monitoring, and treatment for juvenile dermatomyositis. In addition, there has been a steady development of translational studies to determine the genetic determinants, transcriptomic profiles, and immune cell phenotypes in JDM. Recent work toward standardization of disease classification, monitoring, and assessments together with advances in science, technology, and computing will facilitate the advancement toward true precision and personalized medicine in juvenile dermatomyositis in the near future.

Entities:  

Keywords:  Idiopathic inflammatory myopathies; Juvenile dermatomyositis; Precision medicine; Translational research

Year:  2019        PMID: 31813083     DOI: 10.1007/s11926-019-0873-2

Source DB:  PubMed          Journal:  Curr Rheumatol Rep        ISSN: 1523-3774            Impact factor:   4.592


  47 in total

1.  Myogenic Progenitor Cells Exhibit Type I Interferon-Driven Proangiogenic Properties and Molecular Signature During Juvenile Dermatomyositis.

Authors:  Cyril Gitiaux; Claire Latroche; Michèle Weiss-Gayet; Mathieu P Rodero; Darragh Duffy; Brigitte Bader-Meunier; Christophe Glorion; Patrick Nusbaum; Christine Bodemer; Guy Mouchiroud; Jamel Chelly; Stéphane Germain; Isabelle Desguerre; Bénédicte Chazaud
Journal:  Arthritis Rheumatol       Date:  2017-11-28       Impact factor: 10.995

2.  Dysregulated NK cell PLCγ2 signaling and activity in juvenile dermatomyositis.

Authors:  Allison A Throm; Joshua B Alinger; Jeanette T Pingel; Allyssa L Daugherty; Lauren M Pachman; Anthony R French
Journal:  JCI Insight       Date:  2018-11-15

3.  Long-term outcome in patients with juvenile dermatomyositis: a cross-sectional follow-up study.

Authors:  P Mathiesen; H Hegaard; T Herlin; M Zak; F K Pedersen; S Nielsen
Journal:  Scand J Rheumatol       Date:  2011-11-01       Impact factor: 3.641

4.  Anti-Ro52 autoantibodies are associated with interstitial lung disease and more severe disease in patients with juvenile myositis.

Authors:  Sara Sabbagh; Iago Pinal-Fernandez; Lisa G Rider; Andrew Lee Mammen; Takayuki Kishi; Ira N Targoff; Frederick W Miller
Journal:  Ann Rheum Dis       Date:  2019-04-24       Impact factor: 19.103

Review 5.  Rituximab in the treatment of inflammatory myopathies: a review.

Authors:  Serena Fasano; Patrick Gordon; Raouf Hajji; Esthela Loyo; David A Isenberg
Journal:  Rheumatology (Oxford)       Date:  2016-04-27       Impact factor: 7.580

6.  Prednisone versus prednisone plus ciclosporin versus prednisone plus methotrexate in new-onset juvenile dermatomyositis: a randomised trial.

Authors:  Nicolino Ruperto; Angela Pistorio; Sheila Oliveira; Francesco Zulian; Ruben Cuttica; Angelo Ravelli; Michel Fischbach; Bo Magnusson; Gary Sterba; Tadej Avcin; Karine Brochard; Fabrizia Corona; Frank Dressler; Valeria Gerloni; Maria T Apaz; Claudia Bracaglia; Adriana Cespedes-Cruz; Rolando Cimaz; Gerard Couillault; Rik Joos; Pierre Quartier; Ricardo Russo; Marc Tardieu; Nico Wulffraat; Blanca Bica; Pavla Dolezalova; Virginia Ferriani; Berit Flato; Ana G Bernard-Medina; Troels Herlin; Maria Trachana; Antonella Meini; Emma Allain-Launay; Clarissa Pilkington; Veronika Vargova; Carine Wouters; Simona Angioloni; Alberto Martini
Journal:  Lancet       Date:  2015-11-30       Impact factor: 79.321

7.  The Childhood Arthritis and Rheumatology Research Alliance Consensus Treatment Plans: Toward Comparative Effectiveness in the Pediatric Rheumatic Diseases.

Authors:  Sarah Ringold; Peter A Nigrovic; Brian M Feldman; George A Tomlinson; Emily von Scheven; Carol A Wallace; Adam M Huber; Laura E Schanberg; Suzanne C Li; Pamela F Weiss; Robert C Fuhlbrigge; Esi M Morgan; Yukiko Kimura
Journal:  Arthritis Rheumatol       Date:  2018-03-31       Impact factor: 10.995

8.  Development of an internationally agreed minimal dataset for juvenile dermatomyositis (JDM) for clinical and research use.

Authors:  Liza J McCann; Jamie J Kirkham; Lucy R Wedderburn; Clarissa Pilkington; Adam M Huber; Angelo Ravelli; Duncan Appelbe; Paula R Williamson; Michael W Beresford
Journal:  Trials       Date:  2015-06-12       Impact factor: 2.279

9.  Galectin-9 and CXCL10 as Biomarkers for Disease Activity in Juvenile Dermatomyositis: A Longitudinal Cohort Study and Multicohort Validation.

Authors:  Judith Wienke; Felicitas Bellutti Enders; Johan Lim; Jorre S Mertens; Luuk L van den Hoogen; Camiel A Wijngaarde; Joo Guan Yeo; Alain Meyer; Henny G Otten; Ruth D E Fritsch-Stork; Sylvia S M Kamphuis; Esther P A H Hoppenreijs; Wineke Armbrust; J Merlijn van den Berg; Petra C E Hissink Muller; Janneke Tekstra; Jessica E Hoogendijk; Claire T Deakin; Wilco de Jager; Joël A G van Roon; W Ludo van der Pol; Kiran Nistala; Clarissa Pilkington; Marianne de Visser; Thaschawee Arkachaisri; Timothy R D J Radstake; Anneke J van der Kooi; Stefan Nierkens; Lucy R Wedderburn; Annet van Royen-Kerkhof; Femke van Wijk
Journal:  Arthritis Rheumatol       Date:  2019-03-12       Impact factor: 10.995

Review 10.  Consensus-based recommendations for the management of juvenile dermatomyositis.

Authors:  Felicitas Bellutti Enders; Brigitte Bader-Meunier; Eileen Baildam; Tamas Constantin; Pavla Dolezalova; Brian M Feldman; Pekka Lahdenne; Bo Magnusson; Kiran Nistala; Seza Ozen; Clarissa Pilkington; Angelo Ravelli; Ricardo Russo; Yosef Uziel; Marco van Brussel; Janjaap van der Net; Sebastiaan Vastert; Lucy R Wedderburn; Nicolaas Wulffraat; Liza J McCann; Annet van Royen-Kerkhof
Journal:  Ann Rheum Dis       Date:  2016-08-11       Impact factor: 19.103

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