Literature DB >> 31612561

Respiratory assessment in a spinal muscular atrophy infant treated with nusinersen.

Kazuya Ogawa1, Kazuo Okanari1, Osamu Kobayashi1, Misaki Nakashima2, Kenji Ihara1.   

Abstract

Entities:  

Keywords:  nusinersen; spinal muscular atrophy; spontaneous respiration rate; tracheostomy; ventilator

Mesh:

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Year:  2019        PMID: 31612561     DOI: 10.1111/ped.13931

Source DB:  PubMed          Journal:  Pediatr Int        ISSN: 1328-8067            Impact factor:   1.524


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  2 in total

Review 1.  Changes in Ventilatory Support Requirements of Spinal Muscular Atrophy (SMA) Patients Post Gene-Based Therapies.

Authors:  Panagiota Panagiotou; Christina Kanaka-Gantenbein; Athanasios G Kaditis
Journal:  Children (Basel)       Date:  2022-08-11

2.  Successful weaning from mechanical ventilation in a patient with SMA type 1 treated with nusinersen.

Authors:  Jiwon Lee; Se Eun Park; Dajeong Lee; Joo Young Song; Jeehun Lee
Journal:  Ann Clin Transl Neurol       Date:  2021-02-22       Impact factor: 4.511

  2 in total

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