Literature DB >> 31477379

Population-Based Newborn Screening for Mucopolysaccharidosis Type II in Illinois: The First Year Experience.

Barbara K Burton1, George E Hoganson2, Julie Fleischer3, Dorothy K Grange4, Stephen R Braddock5, Rachel Hickey6, Lauren Hitchins7, Daniel Groepper3, Katherine M Christensen5, Amelia Kirby5, Conny Moody8, Heather Shryock8, Laura Ashbaugh8, Rong Shao9, Khaja Basheeruddin9.   

Abstract

OBJECTIVES: To assess the outcome of population-based newborn screening for mucopolysaccharidosis type II (MPS II) during the first year of screening in Illinois. STUDY
DESIGN: Tandem mass spectrometry was used to measure iduronate-2-sulfatase (I2S) activity in dried blood spot specimens obtained from 162 000 infant samples sent to the Newborn Screening Laboratory of the Illinois Department of Public Health in Chicago.
RESULTS: One case of MPS II and 14 infants with pseudodeficiency for I2S were identified.
CONCLUSIONS: Newborn screening for MPS II by measurement of I2S enzyme activity was successfully integrated into the statewide newborn screening program in Illinois.
Copyright © 2019 Elsevier Inc. All rights reserved.

Entities:  

Keywords:  iduronate-2-sulfatase; pseudodeficiency

Year:  2019        PMID: 31477379     DOI: 10.1016/j.jpeds.2019.07.053

Source DB:  PubMed          Journal:  J Pediatr        ISSN: 0022-3476            Impact factor:   4.406


  5 in total

1.  Incorporation of Second-Tier Biomarker Testing Improves the Specificity of Newborn Screening for Mucopolysaccharidosis Type I.

Authors:  Dawn S Peck; Jean M Lacey; Amy L White; Gisele Pino; April L Studinski; Rachel Fisher; Ayesha Ahmad; Linda Spencer; Sarah Viall; Natalie Shallow; Amy Siemon; J Austin Hamm; Brianna K Murray; Kelly L Jones; Dimitar Gavrilov; Devin Oglesbee; Kimiyo Raymond; Dietrich Matern; Piero Rinaldo; Silvia Tortorelli
Journal:  Int J Neonatal Screen       Date:  2020-02-07

2.  Newborn screening for Morquio disease and other lysosomal storage diseases: results from the 8-plex assay for 70,000 newborns.

Authors:  Yin-Hsiu Chien; Ni-Chung Lee; Pin-Wen Chen; Hui-Ying Yeh; Michael H Gelb; Pao-Chin Chiu; Shao-Yin Chu; Chen-Hao Lee; An-Ru Lee; Wuh-Liang Hwu
Journal:  Orphanet J Rare Dis       Date:  2020-02-03       Impact factor: 4.123

3.  A new strategy of desensitization in mucopolysaccharidosis type II disease treated with idursulfase therapy: A case report and review of the literature.

Authors:  Vincenza Gragnaniello; Silvia Carraro; Laura Rubert; Daniela Gueraldi; Chiara Cazzorla; Pamela Massa; Stefania Zanconato; Alberto B Burlina
Journal:  Mol Genet Metab Rep       Date:  2022-05-05

Review 4.  Diagnosis of Mucopolysaccharidoses.

Authors:  Francyne Kubaski; Fabiano de Oliveira Poswar; Kristiane Michelin-Tirelli; Maira Graeff Burin; Diana Rojas-Málaga; Ana Carolina Brusius-Facchin; Sandra Leistner-Segal; Roberto Giugliani
Journal:  Diagnostics (Basel)       Date:  2020-03-22

5.  Newborn Screening for Mucopolysaccharidosis Type II in Illinois: An Update.

Authors:  Barbara K Burton; Rachel Hickey; Lauren Hitchins
Journal:  Int J Neonatal Screen       Date:  2020-09-03
  5 in total

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